Differential integrity of TALE nuclease genes following adenoviral and lentiviral vector gene transfer into human cells M Holkers, I Maggio, J Liu, JM Janssen, F Miselli, C Mussolino, A Recchia, ... Nucleic acids research 41 (5), e63-e63, 2013 | 384 | 2013 |
Adeno-associated virus: from defective virus to effective vector MAFV Gonçalves Virology journal 2, 1-17, 2005 | 384 | 2005 |
Adenoviral vector DNA for accurate genome editing with engineered nucleases M Holkers, I Maggio, SFD Henriques, JM Janssen, T Cathomen, ... Nature methods 11 (10), 1051-1057, 2014 | 182 | 2014 |
Genome editing at the crossroads of delivery, specificity, and fidelity I Maggio, MAFV Gonçalves Trends in biotechnology 33 (5), 280-291, 2015 | 171 | 2015 |
Adenovirus: from foe to friend MAFV Gonçalves, AAF de Vries Reviews in medical virology 16 (3), 167-186, 2006 | 167 | 2006 |
Adenoviral vector delivery of RNA-guided CRISPR/Cas9 nuclease complexes induces targeted mutagenesis in a diverse array of human cells I Maggio, M Holkers, J Liu, JM Janssen, X Chen, MAFV Gonçalves Scientific reports 4 (1), 5105, 2014 | 165 | 2014 |
Engineered viruses as genome editing devices X Chen, MAFV Gonçalves Molecular Therapy 24 (3), 447-457, 2016 | 149 | 2016 |
Probing the impact of chromatin conformation on genome editing tools X Chen, M Rinsma, JM Janssen, J Liu, I Maggio, MAFV Gonçalves Nucleic acids research 44 (13), 6482-6492, 2016 | 147 | 2016 |
Myogenic properties of human mesenchymal stem cells derived from three different sources AS De La Garza-Rodea, I Van Der Velde-Van Dijke, H Boersma, ... Cell transplantation 21 (1), 153-173, 2012 | 109 | 2012 |
Human mesenchymal stem cells ectopically expressing full-length dystrophin can complement Duchenne muscular dystrophy myotubes by cell fusion MAFV Goncalves, AAF de Vries, M Holkers, MJM van de Watering, ... Human Molecular Genetics 15 (2), 213-221, 2006 | 105 | 2006 |
In trans paired nicking triggers seamless genome editing without double-stranded DNA cutting X Chen, JM Janssen, J Liu, I Maggio, AEJ ‘t Jong, HMM Mikkers, ... Nature Communications 8 (1), 657, 2017 | 88 | 2017 |
Selection-free gene repair after adenoviral vector transduction of designer nucleases: rescue of dystrophin synthesis in DMD muscle cell populations I Maggio, L Stefanucci, JM Janssen, J Liu, X Chen, V Mouly, ... Nucleic acids research 44 (3), 1449-1470, 2016 | 84 | 2016 |
Adenoviral vectors encoding CRISPR/Cas9 multiplexes rescue dystrophin synthesis in unselected populations of DMD muscle cells I Maggio, J Liu, JM Janssen, X Chen, MAFV Gonçalves Scientific reports 6 (1), 37051, 2016 | 78 | 2016 |
Long-term contribution of human bone marrow mesenchymal stromal cells to skeletal muscle regeneration in mice AS De La Garza-Rodea, I Van Der Velde, H Boersma, MAFV Gonçalves, ... Cell Transplantation 20 (2), 217-232, 2011 | 78 | 2011 |
Stimulation of homology-directed gene targeting at an endogenous human locus by a nicking endonuclease GP van Nierop, AAF de Vries, M Holkers, KR Vrijsen, MAFV Goncalves Nucleic acids research 37 (17), 5725-5736, 2009 | 73 | 2009 |
Endowing human adenovirus serotype 5 vectors with fiber domains of species B greatly enhances gene transfer into human mesenchymal stem cells S Knaän‐Shanzer, MJM van de Watering, I van der Velde, ... Stem Cells 23 (10), 1598-1607, 2005 | 71 | 2005 |
Targeted gene addition in human epithelial stem cells by zinc-finger nuclease-mediated homologous recombination A Coluccio, F Miselli, A Lombardo, A Marconi, GM Tagliazucchi, ... Molecular Therapy 21 (9), 1695-1704, 2013 | 64 | 2013 |
Histone deacetylase inhibition activates transgene expression from integration-defective lentiviral vectors in dividing and non-dividing cells LPL Pelascini, JM Janssen, MAFV Gonçalves Human gene therapy 24 (1), 78-96, 2012 | 63 | 2012 |
A concise peer into the background, initial thoughts and practices of human gene therapy MAFV Goncalves Bioessays 27 (5), 506-517, 2005 | 58 | 2005 |
The chromatin structure of CRISPR-Cas9 target DNA controls the balance between mutagenic and homology-directed gene-editing events JM Janssen, X Chen, J Liu, MAFV Gonçalves Molecular Therapy-Nucleic Acids 16, 141-154, 2019 | 54 | 2019 |