| Prevention and reversal of severe mitochondrial cardiomyopathy by gene therapy in a mouse model of Friedreich's ataxia M Perdomini, B Belbellaa, L Monassier, L Reutenauer, N Messaddeq, ... Nature medicine 20 (5), 542-547, 2014 | 253 | 2014 |
| In vivo gene regulation using tetracycline-regulatable systems K Stieger, B Belbellaa, C Le Guiner, P Moullier, F Rolling Advanced drug delivery reviews 61 (7-8), 527-541, 2009 | 173 | 2009 |
| Detection of intact rAAV particles up to 6 years after successful gene transfer in the retina of dogs and primates K Stieger, J Schroeder, N Provost, A Mendes-Madeira, B Belbellaa, ... Molecular Therapy 17 (3), 516-523, 2009 | 103 | 2009 |
| High levels of frataxin overexpression lead to mitochondrial and cardiac toxicity in mouse models B Belbellaa, L Reutenauer, N Messaddeq, L Monassier, H Puccio Molecular Therapy-Methods & Clinical Development 19, 120-138, 2020 | 61 | 2020 |
| Correction of half the cardiomyocytes fully rescue Friedreich ataxia mitochondrial cardiomyopathy through cell-autonomous mechanisms B Belbellaa, L Reutenauer, L Monassier, H Puccio Human Molecular Genetics 28 (8), 1274-1285, 2019 | 30 | 2019 |
| Structure comparison of the chimeric AAV2. 7m8 vector with parental AAV2 A Bennett, A Keravala, V Makal, J Kurian, B Belbellaa, R Aeran, YS Tseng, ... Journal of structural biology 209 (2), 107433, 2020 | 27 | 2020 |
| High levels of frataxin overexpression leads to mitochondrial and cardiac toxicity in mouse models B Belbellaa, L Reutenauer, N Messaddeq, L Monassier, H Puccio BioRxiv, 2020.03. 31.015255, 2020 | 4 | 2020 |
| Neonatal systemic delivery of scAAV9 in rodents and large animals results in gene transfer to RPE cells in the retina B Joussemet, B Belbellaa, A Mendes-Madeira, T Bucher, D Briot-Nivard, ... Experimental Eye Research 93 (4), 491-502, 2011 | 4 | 2011 |
| Correction of Mitochondrial Cardiomyopathy Associated with Friedreich Ataxia in a Transgenic Model by Gene Therapy B Belbellaa, M Perdomini, L Monassier, L Reutenauer, N Messaddeq, ... Molecular Therapy 21, S106-S106, 2013 | 2 | 2013 |
| Novel Capsid LSV1 Has a Unique 3D Structure at the Loop Substitution Area-Confers Superior Retinal Transduction from Intravitreal Injection CK Baker, A Bennett, B Belbellaa, J Nieves, A Tai, R NcKenna, D Cepeda, ... 2022 ASGCT Annual Meeting Abstracts. Molecular Therapy 30, 575, 2022 | 1 | 2022 |
| Feasibility of gene therapy for Friedreich Ataxia-associated cardiomyopathy in non-human primates: Evaluation of delivery route, biodistribution and expression following AAVRh … B Belbellaa, V Bonnamain, SM Kaminsky, D Sondhi, J Rosenberg, ... HUMAN GENE THERAPY 30 (11), A158-A159, 2019 | 1 | 2019 |
| Toward gene therapy for Friedreich ataxia-associated cardiomyopathy B Belbellaa, H Puccio Medecine sciences: M/S 30 (10), 842-845, 2014 | 1 | 2014 |
| Vers une thérapie génique pour la cardiomyopathie associée à l’ataxie de Friedreich B Belbellaa, H Puccio médecine/sciences 30 (10), 842-845, 2014 | 1 | 2014 |
| AAV Based Gene Therapy Rescues the Murine Cardiac Phenotype Associated with Friedreich's Ataxia H Puccio, B Belbellaa, M Perdomini, N Cartier, P Aubourg MOLECULAR THERAPY 20, S125-S125, 2012 | 1 | 2012 |
| High Affinity Cardiac Gene Transfer Mediated by Systemic Delivery of AAVrh. 10 Vectors BP De, JB Rosenberg, C Jose, A Chen, E Fung, J Babich, DJ Ballon, ... MOLECULAR THERAPY 29 (4), 181-182, 2021 | | 2021 |
| Biodistribution and pharmacokinetics of AAVRh. 10-A1AT mediated gene therapy in humanized-liver mice as a predictor of A1AT human expression levels following intravenous delivery D Cepeda, B Belbellaa, E Yeh, A Rosario, J Nieves, DO Morales, ... HUMAN GENE THERAPY 30 (11), A143-A143, 2019 | | 2019 |
| Correction of Half the Cardiomyocytes is Sufficient to Obtain Full Functional Rescue of a Severe Mitochondrial Cardiomyopathy through Cell-Autonomous Mechanisms B Belbellaa, L Reutenauer, L Monassier, H Puccio MOLECULAR THERAPY 26 (5), 349-350, 2018 | | 2018 |
| Towards gene therapy for the cardiomyopathy associated with Friedreich's ataxia B Belbellaa, H Puccio M S-MEDECINE SCIENCES 30 (10), 842-845, 2014 | | 2014 |
| 0300: Systemic delivery of AAVrh10 expressing frataxin corrects the severe mitochondrial cardiomyopathy of frataxin deficient mice B Belbellaa, M Perdomini, L Monassier, P Aubourg, H Puccio Archives of Cardiovascular Diseases Supplements 6, 49, 2014 | | 2014 |
| 277. AAV-Mediated Direct Somatic Genetic Correction of Epidermolysis Bullosa B Belbellaa, M Perdomini, L Monassier, L Reutenauer, N Messaddeq, ... Molecular Therapy 21, 1, 2013 | | 2013 |
