In vivo genome editing restores haemostasis in a mouse model of haemophilia H Li, V Haurigot, Y Doyon, T Li, SY Wong, AS Bhagwat, N Malani, ... Nature 475 (7355), 217-221, 2011 | 751 | 2011 |
Host cell factors in HIV replication: meta-analysis of genome-wide studies FD Bushman, N Malani, J Fernandes, I D'Orso, G Cagney, TL Diamond, ... PLoS pathogens 5 (5), e1000437, 2009 | 525 | 2009 |
Feasibility of blood testing combined with PET-CT to screen for cancer and guide intervention AM Lennon, AH Buchanan, I Kinde, A Warren, A Honushefsky, AT Cohain, ... Science 369 (6499), eabb9601, 2020 | 467 | 2020 |
A modified γ-retrovirus vector for X-linked severe combined immunodeficiency S Hacein-Bey-Abina, SY Pai, HB Gaspar, M Armant, CC Berry, S Blanche, ... New England Journal of Medicine 371 (15), 1407-1417, 2014 | 460 | 2014 |
Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome SHB Abina, HB Gaspar, J Blondeau, L Caccavelli, S Charrier, K Buckland, ... Jama 313 (15), 1550-1563, 2015 | 430 | 2015 |
Genomic safe harbors permit high β-globin transgene expression in thalassemia induced pluripotent stem cells EP Papapetrou, G Lee, N Malani, M Setty, I Riviere, LMS Tirunagari, ... Nature biotechnology 29 (1), 73-78, 2011 | 370 | 2011 |
The host genomic environment of the provirus determines the abundance of HTLV-1–infected T-cell clones NA Gillet, N Malani, A Melamed, N Gormley, R Carter, D Bentley, C Berry, ... Blood, The Journal of the American Society of Hematology 117 (11), 3113-3122, 2011 | 317 | 2011 |
HIV integration targeting: a pathway involving Transportin-3 and the nuclear pore protein RanBP2 KE Ocwieja, TL Brady, K Ronen, A Huegel, SL Roth, T Schaller, ... PLoS pathogens 7 (3), e1001313, 2011 | 267 | 2011 |
Assessing the potential for AAV vector genotoxicity in a murine model H Li, N Malani, SR Hamilton, A Schlachterman, G Bussadori, ... Blood, The Journal of the American Society of Hematology 117 (12), 3311-3319, 2011 | 266 | 2011 |
piggyBac transposase tools for genome engineering X Li, ER Burnight, AL Cooney, N Malani, T Brady, JD Sander, J Staber, ... Proceedings of the National Academy of Sciences 110 (25), E2279-E2287, 2013 | 252 | 2013 |
BET proteins promote efficient murine leukemia virus integration at transcription start sites A Sharma, RC Larue, MR Plumb, N Malani, F Male, A Slaughter, JJ Kessl, ... Proceedings of the National Academy of Sciences 110 (29), 12036-12041, 2013 | 207 | 2013 |
Analysis of lentiviral vector integration in HIV+ study subjects receiving autologous infusions of gene modified CD4+ T cells GP Wang, BL Levine, GK Binder, CC Berry, N Malani, G McGarrity, ... Molecular therapy 17 (5), 844-850, 2009 | 193 | 2009 |
The BET family of proteins targets moloney murine leukemia virus integration near transcription start sites J De Rijck, C de Kogel, J Demeulemeester, S Vets, S El Ashkar, N Malani, ... Cell reports 5 (4), 886-894, 2013 | 192 | 2013 |
HIV integration site distributions in resting and activated CD4+ T cells infected in culture T Brady, LM Agosto, N Malani, CC Berry, U O'Doherty, F Bushman Aids 23 (12), 1461-1471, 2009 | 182 | 2009 |
LEDGF hybrids efficiently retarget lentiviral integration into heterochromatin R Gijsbers, K Ronen, S Vets, N Malani, J De Rijck, M McNeely, ... Molecular Therapy 18 (3), 552-560, 2010 | 173 | 2010 |
Dynamics of gene-modified progenitor cells analyzed by tracking retroviral integration sites in a human SCID-X1 gene therapy trial GP Wang, CC Berry, N Malani, P Leboulch, A Fischer, ... Blood, The Journal of the American Society of Hematology 115 (22), 4356-4366, 2010 | 143 | 2010 |
A new class of multimerization selective inhibitors of HIV-1 integrase A Sharma, A Slaughter, N Jena, L Feng, JJ Kessl, HJ Fadel, N Malani, ... PLoS pathogens 10 (5), e1004171, 2014 | 139 | 2014 |
Integration target site selection by a resurrected human endogenous retrovirus T Brady, YN Lee, K Ronen, N Malani, CC Berry, PD Bieniasz, ... Genes & development 23 (5), 633-642, 2009 | 128 | 2009 |
HIV latency and integration site placement in five cell-based models S Sherrill-Mix, MK Lewinski, M Famiglietti, A Bosque, N Malani, ... Retrovirology 10, 1-14, 2013 | 119 | 2013 |
The major cellular sterol regulatory pathway is required for Andes virus infection J Petersen, MJ Drake, EA Bruce, AM Riblett, CA Didigu, CB Wilen, ... PLoS pathogens 10 (2), e1003911, 2014 | 100 | 2014 |