235. The Route of Vector Delivery Impacts the Therapeutic Effects of AAV-Mediated Gene Therapy in Adult Mucopolysaccharidosis IIIB Mice E Ayuso, V Jimenez, J Agudo, V Haurigot, JC Segovia, J Bueren, F Bosch Molecular Therapy 11, 1, 2005 | | 2005 |
236. Bone Marrow-Derived Cells Do Not Contribute to Endocrine Pancreas Regeneration in Diabetic RIP/IGF-I Transgenic Mice E Ayuso, V Jimenez, J Agudo, V Haurigot, JC Segovia, J Bueren, F Bosch Molecular Therapy, 93, 2005 | 2 | 2005 |
302. Molecular AAV Capsid Evolution Is Not Primarily Restricted by Inadvertent Shuffling of the Assembly-Activating Protein AAP S Grosse, M Penaud-Budloo, E Ayuso, D Grimm Molecular Therapy 24, S121, 2016 | | 2016 |
34. Development and Validation of Identity and Homogeneity Assays for AAV Preparations S Pacouret, M Mevel, M Bouzelha, A Maurer, R Shelke, R Xiao, ... Molecular Therapy 24, S15, 2016 | | 2016 |
417. Non-Invasive Monitoring of Insulin-Producing Cells In Vivo with Viral Vectors M Morro, R Lage, A Casellas, V Jimenez, C Mallol, S Marletta, ... Molecular Therapy 20, 1, 2012 | | 2012 |
50. Long-Term Follow-Up of Diabetic Dogs Treated with Adeno-Associated Viral Vectors Encoding for Insulin and Glucokinase V Jimenez, ML Jaen, L Vila, J Rodo, M Garcia, I Elias, L Maggioni, X Leon, ... Molecular Therapy 24, S22, 2016 | | 2016 |
980. Regulation of Cell Surface Expression of Nucleolin by Phosphorylation of Cell Cycle Dependent Kinase CJ Mann, D Callejas, J Montane, E Ayuso, XM Anguela, M Moya, X Leon, ... Molecular Therapy 16, 1, 2008 | | 2008 |
A TELOMERASE GENE THERAPY INTERVENTION IN ADULT/OLD MICE EXTENDS HEALTH-SPAN AND LONGEVITY IN THE ABSENCE OF CANCER BB de Jesus, E Vera, K Schneeberger, E Ayuso, F Bosch, MA Blasco Nature, 2010 | | 2010 |
AAV Gene Therapy For Diabetes Mellitus E Ayuso, V Jimenez, D Callejas, C Mann, F Bosch The Clinibook: Clinical Gene Transfer State of the Art, Cohen-Haguenauer, O …, 0 | 2 | |
AAV-GPseq Analysis of Vectors from HEK293 and BEV/Sf9 Production Platforms Reveals Differential Genome Heterogeneity and Enrichment of Potential Innate Immune DNA Epitopes in … NT Tran, K Weber, S Namkung, E Ayuso, O Adjali, C Robin, E Devine, ... MOLECULAR THERAPY 29 (4), 99-100, 2021 | | 2021 |
AAV-ID: a rapid and robust assay for batch-to-batch consistency evaluation of AAV preparations S Pacouret, M Bouzelha, R Shelke, E Andres-Mateos, R Xiao, A Maurer, ... Molecular Therapy 25 (6), 1375-1386, 2017 | 85 | 2017 |
AAV-Mediated Sulfamidase Expression in the Liver Prevents Development of Somatic Alterations in MPS IIIA Mice A Ruzo, M Garcia, V Haurigot, S Marco, P Villacampa, A Ribera, C Roca, ... Human Gene Therapy 20 (9), 1045-1046, 2009 | 1 | 2009 |
AAV-mediated sulphamidase expression in the liver prevents development of somatic alterations in MPS IIIA mice A Ruzo, M Garcia, V Haurigot, A Chiandetti, XM Anguela, C Roca, X Leon, ... HUMAN GENE THERAPY 19 (10), 1131-1131, 2008 | | 2008 |
AAV9-Based sulfamidase gene transfer reverses somatic and neurological pathology in mpsiiia mice A Ruzo, M Garcia, S Marco, P Villacampa, A Ribera, E Ayuso, V Haurigot, ... HUMAN GENE THERAPY 21 (10), 1389-1389, 2010 | | 2010 |
ABSTRACT 血管内皮細胞成長因子が媒介する膵島の過剰な血管新生および炎症は進行性の β 細胞量減少に寄与する J Agudo, E Ayuso, V Jimenez Diabetes: a journal of the American Diabetes Association 6 (3), 36-38, 2013 | | 2013 |
Accurate identification and quantification of DNA species by next-generation sequencing in adeno-associated viral vectors produced in insect cells M Penaud-Budloo, E Lecomte, A Guy-Duché, S Saleun, A Roulet, ... Human gene therapy methods 28 (3), 148-162, 2017 | 65 | 2017 |
Accurate titration of infectious AAV particles requires measurement of biologically active vector genomes and suitable controls A François, M Bouzelha, E Lecomte, F Broucque, M Penaud-Budloo, ... Molecular Therapy Methods & Clinical Development 10, 223-236, 2018 | 58 | 2018 |
Additional Neuroprotective Effects Of Proinsulin On Vision And Retinal Structure In The Rd10 Mouse Model Of Retinitis Pigmentosa EJ de la Rosa, N Forns, M Marchena, A Hernandez-Pinto, R Steel, ... Investigative Ophthalmology & Visual Science 53 (14), 6447-6447, 2012 | | 2012 |
Adenovirus-mediated gene transfer to mouse and dog pancreas in vivo E Ayuso, M Chillon, F Garcia, J Agudo, A Andaluz, V Haurigot, A Bosch, ... Molecular Therapy 9, S66-S66, 2004 | | 2004 |
Advancing Liver Gene Therapy: Enhanced Transduction with GalNAc-Bioconjugated rAAV Capsids PA Lalys, A Bourdon, M Bouzelha, D Alvarez-Dorta, K Pavageau, T Girard, ... bioRxiv, 2024.07. 25.605063, 2024 | | 2024 |