1087. Balloon Occlusion Catheter-Based Delivery of HDAd into the Nonhuman Primate Liver Results in Stable, High Level Transgene Expression with Minimal Toxicity N Brunetti-Pierri, G Stapleton, D Palmer, Y Zuo, A Beaudet, C Mullins, ... Molecular Therapy 13, S417, 2006 | 1 | 2006 |
15q13q14 deletions: phenotypic characterization and molecular delineation by comparative genomic hybridization N Brunetti‐Pierri, T Sahoo, S Frioux, C Chinault, R Zascavage, ... American Journal of Medical Genetics Part A 146 (15), 1933-1941, 2008 | 14 | 2008 |
163. Phenotypic correction of a hemophilia B dog following systemic administration of a helper-dependent ad vector encoding canine coagulation factor IX N Brunetti-pierri, D Palmer, TC Nichols, AL Beaudet, P Ng Molecular Therapy 9 (S1), S62, 2004 | 1 | 2004 |
174. High efficiency HDAd-mediated hepatic transduction can be achieved by delivery into the surgically isolated liver of nonhuman primates N Brunetti-pierri, W Cioffi, D Iannitti, T Ng, D Palmer, A Beaudet, ... Molecular Therapy 9 (S1), S66, 2004 | | 2004 |
19. Aortic root dilatation: a previously unrecognized clinical feature of mitochondrial cytopathies N Brunetti-Pierri, N Fouladi, J Towbin, JL Jefferies, VR Sutton, J Belmont, ... Mitochondrion 1 (9), 65, 2009 | | 2009 |
213. Improving the Therapeutic Index of Helper-Dependent Adenoviral Vector for Crigler-Najjar Gene Therapy D Dimmock, N Brunetti-Pierri, V Mane, D Palmer, A Beaudet, P Ng Molecular Therapy 13, S82, 2006 | | 2006 |
3 Helper-Dependent N Brunetti-Pierri, P Ng Therapeutic Applications of Adenoviruses, 59, 2016 | 1 | 2016 |
30-year follow-up of a patient with classic citrullinemia N Brunetti-Pierri, KM Lamance, RA Lewis, WJ Craigen Molecular Genetics and Metabolism 106 (2), 248-250, 2012 | 14 | 2012 |
372. Prevalence of Anti-AAV8 Neutralizing Antibodies and ARSB Cross-Reactive Immunologic Material in MPS VI Patients Candidates for a Gene Therapy Trial R Ferla, P Claudiani, M Savarese, K Kozarsky, R Parini, M Scarpa, ... Molecular Therapy 23, S148, 2015 | | 2015 |
428. The Development of Non-Viral Vectors for Choroideremia A Puppo, G Cesi, DJ Palmer, P Piccolo, RJ Parks, P Ng, N Brunetti-Pierri, ... Molecular Therapy 20, 1, 2012 | | 2012 |
454. AAV Mediated Gene Transfer to Skeletal Muscle Results in Sustained Reduction of Hyperbilirubinemia in an Animal Model of Crigler-Najjar Syndrome Type N Pastore, RM Sepe, F Vetrini, E Nusco, A Auricchio, N Brunetti-Pierri Molecular Therapy 19, 1, 2011 | | 2011 |
47. Gene Transfer-Mediated Diversion Towards Non-Toxic Metabolites for Therapy of Primary Hyperoxaluria Type 1 N Brunetti-Pierri, R Castello, P Annunziata, R Borzone Molecular Therapy 24, S21, 2016 | | 2016 |
607. Long-Term Phenotypic Correction of Canine Hemophilia B Following Systemic Administration of Helper Dependent Adenoviral Vector N Brunetti-Pierri, T Nichols, D Palmer, S McCorquodale, E Merricks, ... Molecular Therapy 11, 235-235, 2005 | | 2005 |
683. Bronchoscope-Guided, Targeted Lobar Aersolization of HDAd into the Lungs of Nonhuman Primate Results in Exceedingly High Pulmonary Transduction Uniformally throughout the … P Hiatt, N Brunetti-Pierri, R McConnell, D Palmer, J Katkin, D Dimmock, ... Molecular Therapy 13, S264, 2006 | 2 | 2006 |
703. Liver-Directed Gene Therapy for Primary Hyperoxaluria Type 1 R Castello, R Borzone, P Annunziata, P Piccolo, N Brunetti-Pierri Molecular Therapy 23, S280, 2015 | | 2015 |
789. Hydrodynamic Injection of Helper Dependent Adenoviral Vectors Increases Liver Transduction Efficiency and Decreases Acute Inflammatory Response N Brunetti-pierri, V Mane, D Palmer, AL Beaudet, P Ng Molecular Therapy 9 (S1), S299, 2004 | 1 | 2004 |
815. Aerosol Delivery of Helper-Dependent Adenoviral Vector into Nonhuman Primate Lungs Results in High Efficiency Pulmonary Transduction with Minimal Toxicity P Hiatt, N Brunetti-Pierri, D Koehler, R McConnell, J Katkin, D Palmer, ... Molecular Therapy 11 (S1), S317, 2005 | 12 | 2005 |
903. Ornithine Transacarbamylase Deficiency Correction with Low Dose of Helper-Dependent Adenoviral Vector N Brunetti-Pierri, C Clarke, V Mane, D Palmer, P Ng, W O'brien, B Lee Molecular Therapy 11 (S1), S349, 2005 | | 2005 |
903. Pulmonary Transduction in Nonhuman Primates by HDAd: Duration of Transgene Expression and Vector Re-Administration P Hiatt, N Brunetti-Pierri, R McConnell, DJ Palmer, F Vetrini, N Grove, ... Molecular Therapy 16, 1, 2008 | 2 | 2008 |
904. High Efficiency Hepatic Transduction and Long-Term Transgene Expression by Delivering Helper-Dependent Adenoviral Vectors into the Surgically Isolated Liver of Nonhuman … N Brunetti-Pierri, T Ng, D Iannitti, W Cioffi, D Palmer, A Beaudet, ... Molecular Therapy 11, 350-350, 2005 | | 2005 |