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Polynucleotides encoding citrin for the treatment of Citrullinemia type 2 P Martini, S Hoge, K Benenato, V Presnyak, I McFadyen, ... US Patent 10,993,918, 2021 | 52 | 2021 |
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Polynucleotides encoding cystic fibrosis transmembrane conductance regulator for the treatment of cystic fibrosis K Benenato, S Hoge, I McFadyen, V Presnyak, P Martini, ... US Patent 11,801,227, 2023 | 45 | 2023 |
Polynucleotides Encoding Acyl-CoA Dehydrogenase, Very Long-Chain for the Treatment of Very Long-Chain Acyl-CoA Dehydrogenase Deficiency P Martini, S Hoge, K Benenato, V Presnyak, I McFadyen, ... US Patent App. 16/302,298, 2019 | 44 | 2019 |
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Polynucleotides encoding porphobilinogen deaminase for the treatment of acute intermittent porphyria P Martini, S Hoge, K Benenato, V Presnyak, L Jiang, I McFadyen, ... US Patent App. 16/302,339, 2020 | 43 | 2020 |
Polynucleotides Encoding Lipoprotein Lipase for the Treatment of Hyperlipidemia K Benenato, S Hoge, P Martini, I McFadyen, V Presnyak, ... US Patent App. 16/302,368, 2019 | 43 | 2019 |
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Polynucleotides encoding galactose-1-phosphate uridylyltransferase for the treatment of galactosemia type 1 P Martini, S Hoge, K Benenato, V Presnyak, I Mcfadyen, ... US Patent 11,001,861, 2021 | 42 | 2021 |