受强制性开放获取政策约束的文章 - Pasqualina (Lina) Colella了解详情
无法在其他位置公开访问的文章：3 篇
Efficient gene delivery to the cone-enriched pig retina by dual AAV vectors
P Colella, I Trapani, G Cesi, A Sommella, A Manfredi, A Puppo, C Iodice, ...
Gene therapy 21 (4), 450-456, 2014
强制性开放获取政策： US National Institutes of Health, Fondazione Telethon, Italy, European …
Gene therapy for Pompe disease: the time is now
P Colella, F Mingozzi
Human gene therapy 30 (10), 1245-1262, 2019
强制性开放获取政策： European Commission
Photoreceptor degeneration in mice: adeno-associated viral vector-mediated delivery of erythropoietin
P Colella, A Auricchio
Tissue-Protective Cytokines: Methods and Protocols, 237-263, 2013
强制性开放获取政策： Fondazione Telethon, Italy
可在其他位置公开访问的文章：24 篇
TFEB links autophagy to lysosomal biogenesis
C Settembre, C Di Malta, VA Polito, MG Arencibia, F Vetrini, S Erdin, ...
science 332 (6036), 1429-1433, 2011
强制性开放获取政策： US National Institutes of Health, Fondazione Telethon, Italy
Emerging issues in AAV-mediated in vivo gene therapy
P Colella, G Ronzitti, F Mingozzi
Molecular Therapy-Methods & Clinical Development 8, 87-104, 2018
强制性开放获取政策： European Commission
Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice
M Allocca, M Doria, M Petrillo, P Colella, M Garcia-Hoyos, D Gibbs, ...
The Journal of clinical investigation 118 (5), 1955-1964, 2008
强制性开放获取政策： US National Institutes of Health
Effective delivery of large genes to the retina by dual AAV vectors
I Trapani, P Colella, A Sommella, C Iodice, G Cesi, S de Simone, ...
EMBO molecular medicine 6 (2), 194-211, 2014
强制性开放获取政策： US National Institutes of Health, Science Foundation Ireland, Fondazione …
Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase
F Puzzo, P Colella, MG Biferi, D Bali, NK Paulk, P Vidal, F Collaud, ...
Science translational medicine 9 (418), eaam6375, 2017
强制性开放获取政策： US National Institutes of Health, European Commission
Improved dual AAV vectors with reduced expression of truncated proteins are safe and effective in the retina of a mouse model of Stargardt disease
I Trapani, E Toriello, S De Simone, P Colella, C Iodice, EV Polishchuk, ...
Human molecular genetics 24 (23), 6811-6825, 2015
强制性开放获取政策： Fondazione Telethon, Italy, European Commission
AAV gene transfer with tandem promoter design prevents anti-transgene immunity and provides persistent efficacy in neonate pompe mice
P Colella, P Sellier, HC Verdera, F Puzzo, L van Wittenberghe, ...
Molecular Therapy-Methods & Clinical Development 12, 85-101, 2019
强制性开放获取政策： European Commission
Gene therapy of inherited retinopathies: a long and successful road from viral vectors to patients
P Colella, A Auricchio
Human gene therapy 23 (8), 796-807, 2012
强制性开放获取政策： US National Institutes of Health, Fondazione Telethon, Italy
Engineering monocyte/macrophage− specific glucocerebrosidase expression in human hematopoietic stem cells using genome editing
SG Scharenberg, E Poletto, KL Lucot, P Colella, A Sheikali, TJ Montine, ...
Nature Communications 11 (1), 3327, 2020
强制性开放获取政策： US National Institutes of Health
Non-erythropoietic erythropoietin derivatives protect from light-induced and genetic photoreceptor degeneration
P Colella, C Iodice, U Di Vicino, I Annunziata, EM Surace, A Auricchio
Human molecular genetics 20 (11), 2251-2262, 2011
强制性开放获取政策： Fondazione Telethon, Italy
Rescue of GSDIII phenotype with gene transfer requires liver-and muscle-targeted GDE expression
P Vidal, S Pagliarani, P Colella, HC Verdera, L Jauze, M Gjorgjieva, ...
Molecular Therapy 26 (3), 890-901, 2018
强制性开放获取政策： Fondazione Telethon, Italy
Myosin7a deficiency results in reduced retinal activity which is improved by gene therapy
P Colella, A Sommella, E Marrocco, U Di Vicino, E Polishchuk, ...
PloS one 8 (8), e72027, 2013
强制性开放获取政策： US National Institutes of Health, Fondazione Telethon, Italy, Government of …
Long-term exposure to Myozyme results in a decrease of anti-drug antibodies in late-onset Pompe disease patients
E Masat, P Laforêt, M De Antonio, G Corre, B Perniconi, N Taouagh, ...
Scientific reports 6 (1), 36182, 2016
强制性开放获取政策： European Commission
AAV-mediated gene supply for treatment of degenerative and neovascular retinal diseases
P Colella, A Auricchio
Current gene therapy 10 (5), 371-380, 2010
强制性开放获取政策： Fondazione Telethon, Italy
Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates
H Costa-Verdera, F Collaud, CR Riling, P Sellier, JML Nordin, ...
Nature Communications 12 (1), 6393, 2021
强制性开放获取政策： European Commission
Gene therapy with secreted acid alpha-glucosidase rescues Pompe disease in a novel mouse model with early-onset spinal cord and respiratory defects
P Colella, P Sellier, MJ Gomez, MG Biferi, G Tanniou, N Guerchet, ...
EBioMedicine 61, 2020
强制性开放获取政策： European Commission
Role of regulatory T cell and effector T cell exhaustion in liver-mediated transgene tolerance in muscle
J Poupiot, HC Verdera, R Hardet, P Colella, F Collaud, L Bartolo, ...
Molecular Therapy-Methods & Clinical Development 15, 83-100, 2019
强制性开放获取政策： European Commission, Agence Nationale de la Recherche
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