| Directly converted astrocytes retain the ageing features of the donor fibroblasts and elucidate the astrocytic contribution to human CNS health and disease N Gatto, C Dos Santos Souza, AC Shaw, SM Bell, MA Myszczynska, ... Aging Cell 20 (1), e13281, 2021 | 49 | 2021 |
| Editor's highlight: embryonic exposure to the environmental neurotoxin BMAA negatively impacts early neuronal development and progression of neurodegeneration in the sod1-g93r … S Powers, S Kwok, E Lovejoy, T Lavin, RB Sher Toxicological Sciences 157 (1), 129-140, 2017 | 30 | 2017 |
| Rett syndrome gene therapy improves survival and ameliorates behavioral phenotypes in MeCP2 null (S51. 002) S Powers, C Miranda, C Dennys-Rivers, A Huffenberger, L Braun, ... Neurology 92 (15_supplement), S51. 002, 2019 | 8 | 2019 |
| Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates S Powers, S Likhite, KK Gadalla, CJ Miranda, AJ Huffenberger, C Dennys, ... Molecular Therapy 31 (9), 2767-2782, 2023 | 7 | 2023 |
| Mechanisms of IRF2BPL-related disorders and identification of a potential therapeutic strategy SS Ray, D Dutta, C Dennys, S Powers, F Roussel, P Lisowski, P Glažar, ... Cell Reports 41 (10), 2022 | 6 | 2022 |
| In vitro modeling as a tool for testing therapeutics for spinal muscular atrophy and IGHMBP2-related disorders JA Sierra-Delgado, S Sinha-Ray, A Kaleem, M Ganjibakhsh, M Parvate, ... Biology 12 (6), 867, 2023 | 4 | 2023 |
| Rett syndrome gene therapy improves survival and ameliorates behavioral phenotypes in MeCP2 null S Powers, C Miranda, C Dennys-Rivers, A Huffenberger, L Braun, ... Oral presentation, 2019 | 3 | 2019 |
| Environmental and Genetic Interactions in a Zebrafish Model of Amyotrophic Lateral Sclerosis S Powers | 1 | 2015 |
| MeCP2 gene therapy ameliorates disease phenotype in mouse model for Pitt Hopkins syndrome CN Dennys, SAD Vermudez, RJM Deacon, JA Sierra-Delgado, K Rich, ... Neurotherapeutics, e00376, 2024 | | 2024 |
| A Novel Gene Therapy for Rett Syndrome through Reactivation of the Silent X Chromosome S Powers, S Lou, S Nardini, S Likhite, J Delgado, A Sierra, M Baird, ... MOLECULAR THERAPY 30 (4), 395-395, 2022 | | 2022 |
| Advancing Treatment and Understanding of Rett Syndrome SL Powers The Ohio State University, 2020 | | 2020 |
| Efficacy and Safety in Mice and Non-Hman Primates of CSF Delivered AVXS-201 for the Treatment of Rett Syndrome K Foust, G Thomsen, M Fugere, L Braun, K Nguyen, S Solano, E Lang, ... MOLECULAR THERAPY 27 (4), 188-188, 2019 | | 2019 |
| A Novel In Vitro Modeling System for the Study of MeCP2 Pathology and Treatment Response SL Powers, K Kinley, R Rodrigo, X Zhang, S Likhite, C Dennys-Rivers, ... MOLECULAR THERAPY 27 (4), 264-264, 2019 | | 2019 |
