| In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy CE Nelson, CH Hakim, DG Ousterout, PI Thakore, EA Moreb, RMC Rivera, ... Science 351 (6271), 403-407, 2016 | 1331 | 2016 |
| Duchenne muscular dystrophy D Duan, N Goemans, S Takeda, E Mercuri, A Aartsma-Rus Nature Reviews Disease Primers 7 (1), 13, 2021 | 686 | 2021 |
| Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy SQ Harper, MA Hauser, C DelloRusso, D Duan, RW Crawford, SF Phelps, ... Nature medicine 8 (3), 253-261, 2002 | 681 | 2002 |
| Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue D Duan, P Sharma, J Yang, Y Yue, L Dudus, Y Zhang, KJ Fisher, ... Journal of virology 72 (11), 8568-8577, 1998 | 653 | 1998 |
| Animal models of Duchenne muscular dystrophy: from basic mechanisms to gene therapy JW McGreevy, CH Hakim, MA McIntosh, D Duan Disease models & mechanisms 8 (3), 195-213, 2015 | 526 | 2015 |
| Endosomal processing limits gene transfer to polarized airway epithelia by adeno-associated virus D Duan, Y Yue, Z Yan, J Yang, JF Engelhardt The Journal of clinical investigation 105 (11), 1573-1587, 2000 | 483 | 2000 |
| Systemic AAV micro-dystrophin gene therapy for Duchenne muscular dystrophy D Duan Molecular Therapy 26 (10), 2337-2356, 2018 | 423 | 2018 |
| Dystrophins carrying spectrin-like repeats 16 and 17 anchor nNOS to the sarcolemma and enhance exercise performance in a mouse model of muscular dystrophy Y Lai, GD Thomas, Y Yue, HT Yang, D Li, C Long, L Judge, B Bostick, ... The Journal of clinical investigation 119 (3), 624-635, 2009 | 422 | 2009 |
| Trans-splicing vectors expand the utility of adeno-associated virus for gene therapy Z Yan, Y Zhang, D Duan, JF Engelhardt Proceedings of the National Academy of Sciences 97 (12), 6716-6721, 2000 | 384 | 2000 |
| Expanding AAV packaging capacity with trans-splicing or overlapping vectors: a quantitative comparison D Duan, Y Yue, JF Engelhardt Molecular therapy 4 (4), 383-391, 2001 | 316 | 2001 |
| Dynamin is required for recombinant adeno-associated virus type 2 infection D Duan, Q Li, AW Kao, Y Yue, JE Pessin, JF Engelhardt Journal of virology 73 (12), 10371-10376, 1999 | 316 | 1999 |
| Contemporary cardiac issues in Duchenne muscular dystrophy EM McNally, JR Kaltman, DW Benson, CE Canter, LH Cripe, D Duan, ... Circulation 131 (18), 1590-1598, 2015 | 294 | 2015 |
| Real-time, noninvasive in vivo assessment of adeno-associated virus-mediated retinal transduction. J Bennett, D Duan, JF Engelhardt, AM Maguire Investigative ophthalmology & visual science 38 (13), 2857-2863, 1997 | 264 | 1997 |
| Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors Y Lai, Y Yue, M Liu, A Ghosh, JF Engelhardt, JS Chamberlain, D Duan Nature biotechnology 23 (11), 1435-1439, 2005 | 247 | 2005 |
| A new dual-vector approach to enhance recombinant adeno-associated virus-mediated gene expression through intermolecular cis activation D Duan, Y Yue, Z Yan, JF Engelhardt Nature medicine 6 (5), 595-598, 2000 | 245 | 2000 |
| Adeno-associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury M Liu, Y Yue, SQ Harper, RW Grange, JS Chamberlain, D Duan Molecular Therapy 11 (2), 245-256, 2005 | 243 | 2005 |
| Polarity influences the efficiency of recombinant adenoassociated virus infection in differentiated airway epithelia D Duan, Y Yue, Z Yan, PB McCray Jr, JF Engelhardt Human gene therapy 9 (18), 2761-2776, 1998 | 243 | 1998 |
| Systemic AAV-9 transduction in mice is influenced by animal age but not by the route of administration B Bostick, A Ghosh, Y Yue, C Long, D Duan Gene therapy 14 (22), 1605-1609, 2007 | 212 | 2007 |
| Evidence for the failure of adeno-associated virus serotype 5 to package a viral genome≥ 8.2 kb Y Lai, Y Yue, D Duan Molecular Therapy 18 (1), 75-79, 2010 | 204 | 2010 |
| A single intravenous injection of adeno-associated virus serotype-9 leads to whole body skeletal muscle transduction in dogs Y Yue, A Ghosh, C Long, B Bostick, BF Smith, JN Kornegay, D Duan Molecular Therapy 16 (12), 1944-1952, 2008 | 191 | 2008 |
