| COL7A1 editing via CRISPR/Cas9 in recessive dystrophic epidermolysis bullosa S Hainzl, P Peking, T Kocher, EM Murauer, F Larcher, M Del Rio, ... Molecular Therapy 25 (11), 2573-2584, 2017 | 106 | 2017 |
| Cut and paste: efficient homology-directed repair of a dominant negative KRT14 mutation via CRISPR/Cas9 nickases T Kocher, P Peking, A Klausegger, EM Murauer, JP Hofbauer, V Wally, ... Molecular Therapy 25 (11), 2585-2598, 2017 | 95 | 2017 |
| 5′ trans-splicing repair of the PLEC1 gene V Wally, A Klausegger, U Koller, H Lochmüller, S Krause, G Wiche, ... Journal of Investigative Dermatology 128 (3), 568-574, 2008 | 91 | 2008 |
| K14 mRNA reprogramming for dominant epidermolysis bullosa simplex V Wally, M Brunner, T Lettner, M Wagner, U Koller, A Trost, EM Murauer, ... Human molecular genetics 19 (23), 4715-4725, 2010 | 75 | 2010 |
| Traceless targeting and isolation of gene-edited immortalized keratinocytes from epidermolysis bullosa simplex patients M Aushev, U Koller, C Mussolino, T Cathomen, J Reichelt Molecular Therapy Methods & Clinical Development 6, 112-123, 2017 | 54 | 2017 |
| QR-313, an antisense oligonucleotide, shows therapeutic efficacy for treatment of dominant and recessive dystrophic epidermolysis bullosa: a preclinical study O Bornert, M Hogervorst, P Nauroy, J Bischof, J Swildens, I Athanasiou, ... Journal of Investigative Dermatology 141 (4), 883-893. e6, 2021 | 49 | 2021 |
| A gene gun-mediated nonviral RNA trans-splicing strategy for Col7a1 repair P Peking, U Koller, S Hainzl, S Kitzmueller, T Kocher, E Mayr, A Nyström, ... Molecular Therapy-Nucleic Acids 5, 2016 | 49 | 2016 |
| Improved double-nicking strategies for COL7A1-editing by homologous recombination T Kocher, RN Wagner, A Klausegger, C Guttmann-Gruber, S Hainzl, ... Molecular Therapy-Nucleic Acids 18, 496-507, 2019 | 47 | 2019 |
| Construction and validation of an RNA trans-splicing molecule suitable to repair a large number of COL7A1 mutations B Tockner, T Kocher, S Hainzl, J Reichelt, JW Bauer, U Koller, ... Gene Therapy 23 (11), 775-784, 2016 | 45 | 2016 |
| Gene editing for skin diseases: designer nucleases as tools for gene therapy of skin fragility disorders OP March, J Reichelt, U Koller Experimental physiology 103 (4), 449-455, 2018 | 41 | 2018 |
| A novel screening system improves genetic correction by internal exon replacement U Koller, V Wally, LG Mitchell, A Klausegger, EM Murauer, E Mayr, ... Nucleic acids research 39 (16), e108-e108, 2011 | 40 | 2011 |
| Gene Editing–Mediated Disruption of Epidermolytic Ichthyosis–Associated KRT10 Alleles Restores Filament Stability in Keratinocytes OP March, T Lettner, A Klausegger, M Ablinger, T Kocher, S Hainzl, ... Journal of Investigative Dermatology 139 (8), 1699-1710. e6, 2019 | 39 | 2019 |
| Predictable CRISPR/Cas9-mediated COL7A1 reframing for dystrophic epidermolysis bullosa T Kocher, OP March, J Bischof, B Liemberger, S Hainzl, A Klausegger, ... Journal of Investigative Dermatology 140 (10), 1985-1993. e5, 2020 | 37 | 2020 |
| Context-dependent strategies for enhanced genome editing of genodermatoses OP March, T Kocher, U Koller Cells 9 (1), 112, 2020 | 35 | 2020 |
| An ex vivo RNA trans‐splicing strategy to correct human generalized severe epidermolysis bullosa simplex P Peking, JS Breitenbach, M Ablinger, WH Muss, FJ Poetschke, T Kocher, ... British Journal of Dermatology 180 (1), 141-148, 2019 | 35 | 2019 |
| Spliceosome-Mediated RNA Trans-Splicing Facilitates Targeted Delivery of Suicide Genes to Cancer Cells C Gruber, IK Gratz, EM Murauer, E Mayr, U Koller, L Bruckner-Tuderman, ... Molecular Cancer Therapeutics 10 (2), 233-241, 2011 | 35 | 2011 |
| Advances in gene/cell therapy in epidermolysis bullosa EM Murauer, U Koller, G Pellegrini, JW Bauer The Keio journal of medicine 64 (2), 21-25, 2015 | 34 | 2015 |
| An RNA-targeted therapy for dystrophic epidermolysis bullosa P Peking, U Koller, B Duarte, R Murillas, S Wolf, T Maetzig, M Rothe, ... Nucleic Acids Research 45 (17), 10259-10269, 2017 | 33 | 2017 |
| RNA‐based therapies for genodermatoses O Bornert, P Peking, J Bremer, U Koller, PC van den Akker, ... Experimental dermatology 26 (1), 3-10, 2017 | 33 | 2017 |
| Considerations for a successful RNA trans-splicing repair of genetic disorders U Koller, V Wally, JW Bauer, EM Murauer Molecular Therapy-Nucleic Acids 3, 2014 | 32 | 2014 |
Johann BauerProfessor für Dermatologie, Universitätsklinikum der Paracelsus Medizinische Privatuniversität在 salk.at 的电子邮件经过验证
