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[HTML][HTML] Hematopoietic stem-cell gene therapy for cerebral adrenoleukodystrophy

F Eichler, C Duncan, PL Musolino… - … England Journal of …, 2017 - Mass Medical Soc
Background In X-linked adrenoleukodystrophy, mutations in ABCD1 lead to loss of function
of the ALD protein. Cerebral adrenoleukodystrophy is characterized by demyelination and …
被引用次数：527 相关文章
[PDF] academia.edu

[PDF][PDF] Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy.

F Eichler, C Duncan, PL Musolino - The New England journal of …, 2017 - academia.edu
BACKGROUND In X-linked adrenoleukodystrophy, mutations in ABCD1 lead to loss of
function of the ALD protein. Cerebral adrenoleukodystrophy is characterized by …

Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy.

F Eichler, C Duncan, PL Musolino… - The New England …, 2017 - europepmc.org
Background In X-linked adrenoleukodystrophy, mutations in ABCD1 lead to loss of function
of the ALD protein. Cerebral adrenoleukodystrophy is characterized by demyelination and …

[引用][C] Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy

F Eichler, C Duncan, PL Musolino, PJ Orchard… - New England Journal …, 2017 - cir.nii.ac.jp
Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy | CiNii Research
CiNii 国立情報学研究所 学術情報ナビゲータ[サイニィ] 詳細へ移動 検索フォームへ移動 論文・データを …

Hematopoietic stem-cell gene therapy for cerebral adrenoleukodystrophy

F Eichler, C Duncan, PL Musolino… - New England Journal …, 2017 - pure.psu.edu
BACKGROUND: In X-linked adrenoleukodystrophy, mutations in ABCD1 lead to loss of
function of the ALD protein. Cerebral adrenoleukodystrophy is characterized by …
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[HTML][HTML] Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy

F Eichler, C Duncan, PL Musolino… - The New England …, 2017 - ncbi.nlm.nih.gov
BACKGROUND In X-linked adrenoleukodystrophy, mutations in ABCD1 lead to loss of
function of the ALD protein. Cerebral adrenoleukodystrophy is characterized by …

Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy

F Eichler, C Duncan, PL Musolino… - The New England …, 2017 - pubmed.ncbi.nlm.nih.gov
Background In X-linked adrenoleukodystrophy, mutations in ABCD1 lead to loss of function
of the ALD protein. Cerebral adrenoleukodystrophy is characterized by demyelination and …

Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy.

F Eichler, C Duncan, P Musolino, P Orchard, S Oliveira… - 2017 - riu.austral.edu.ar
BACKGROUND: In X-linked adrenoleukodystrophy, mutations in ABCD1 lead to loss of
function of the ALD protein. Cerebral adrenoleukodystrophy is characterized by …

Hematopoietic stem-cell gene therapy for cerebral adrenoleukodystrophy

F Eichler, C Duncan, PL Musolino… - New England Journal …, 2017 - experts.umn.edu
BACKGROUND: In X-linked adrenoleukodystrophy, mutations in ABCD1 lead to loss of
function of the ALD protein. Cerebral adrenoleukodystrophy is characterized by …

Hematopoietic stem-cell gene therapy for cerebral adrenoleukodystrophy

F Eichler, C Duncan, PL Musolino… - … England Journal of …, 2017 - pure.johnshopkins.edu
BACKGROUND: In X-linked adrenoleukodystrophy, mutations in ABCD1 lead to loss of
function of the ALD protein. Cerebral adrenoleukodystrophy is characterized by …