[HTML][HTML] Hematopoietic stem cell gene therapy for storage disease: current and new indications

A Biffi - Molecular Therapy, 2017 - cell.com
Lysosomal storage disorders (LSDs) are a broad class of monogenic diseases with an
overall incidence of 1: 7,000 newborns, due to the defective activity of one or more …

[HTML][HTML] Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications

A Biffi - Molecular Therapy, 2017 - Elsevier
Lysosomal storage disorders (LSDs) are a broad class of monogenic diseases with an
overall incidence of 1: 7,000 newborns, due to the defective activity of one or more …

[引用][C] Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications

A Biffi - MOLECULAR THERAPY, 2017 - research.unipd.it
Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications
IRIS IRIS Home Sfoglia Macrotipologie & tipologie Autore Titolo Riviste Serie IT Italiano …

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications

A Biffi - Molecular Therapy, 2017 - search.proquest.com
Lysosomal storage disorders (LSDs) are a broad class of monogenic diseases with an
overall incidence of 1: 7,000 newborns, due to the defective activity of one or more …

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.

A Biffi - Molecular Therapy: the Journal of the American Society …, 2017 - europepmc.org
Lysosomal storage disorders (LSDs) are a broad class of monogenic diseases with an
overall incidence of 1: 7,000 newborns, due to the defective activity of one or more …

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications

A Biffi - Molecular therapy: the journal of the American …, 2017 - pubmed.ncbi.nlm.nih.gov
Lysosomal storage disorders (LSDs) are a broad class of monogenic diseases with an
overall incidence of 1: 7,000 newborns, due to the defective activity of one or more …

[HTML][HTML] Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications

A Biffi - Molecular Therapy, 2017 - ncbi.nlm.nih.gov
Lysosomal storage disorders (LSDs) are a broad class of monogenic diseases with an
overall incidence of 1: 7,000 newborns, due to the defective activity of one or more …

[引用][C] Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications

A Biffi - Molecular Therapy, 2017 - cir.nii.ac.jp