Spinal muscular atrophy: mechanisms and therapeutic strategies

CL Lorson, H Rindt, M Shababi - Human molecular genetics, 2010 - academic.oup.com
Spinal muscular atrophy (SMA) is an autosomal recessive neurodegenerative disorder and
a leading genetic cause of infantile mortality. SMA is caused by mutation or deletion of …

Spinal muscular atrophy: mechanisms and therapeutic strategies

CL Lorson, H Rindt, M Shababi - Human molecular …, 2010 - pubmed.ncbi.nlm.nih.gov
Spinal muscular atrophy (SMA) is an autosomal recessive neurodegenerative disorder and
a leading genetic cause of infantile mortality. SMA is caused by mutation or deletion of …

[PDF][PDF] Spinal muscular atrophy: mechanisms and therapeutic strategies

CL Lorson, H Rindt, M Shababi - 2010 - researchgate.net
Spinal muscular atrophy (SMA) is an autosomal recessive neurodegenerative disorder and
a leading genetic cause of infantile mortality. SMA is caused by mutation or deletion of …

[PDF][PDF] Spinal muscular atrophy: mechanisms and therapeutic strategies

CL Lorson, H Rindt, M Shababi - 2010 - upload.orthobullets.com
Spinal muscular atrophy (SMA) is an autosomal recessive neurodegenerative disorder and
a leading genetic cause of infantile mortality. SMA is caused by mutation or deletion of …

[引用][C] Spinal muscular atrophy: mechanisms and therapeutic strategies

CL Lorson, H Rindt, M Shababi - Human Molecular Genetics, 2010 - cir.nii.ac.jp
Spinal muscular atrophy: mechanisms and therapeutic strategies | CiNii Research CiNii 国立
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[HTML][HTML] Spinal muscular atrophy: mechanisms and therapeutic strategies

CL Lorson, H Rindt, M Shababi - Human Molecular Genetics, 2010 - ncbi.nlm.nih.gov
Spinal muscular atrophy (SMA) is an autosomal recessive neurodegenerative disorder and
a leading genetic cause of infantile mortality. SMA is caused by mutation or deletion of …

Spinal muscular atrophy: mechanisms and therapeutic strategies.

CL Lorson, H Rindt, M Shababi - Human Molecular Genetics, 2010 - europepmc.org
Spinal muscular atrophy (SMA) is an autosomal recessive neurodegenerative disorder and
a leading genetic cause of infantile mortality. SMA is caused by mutation or deletion of …

[引用][C] Spinal muscular atrophy: mechanisms and therapeutic strategies

CL LORSON, H RINDT… - … molecular genetics (Print), 2010 - pascal-francis.inist.fr
Spinal muscular atrophy: mechanisms and therapeutic strategies CNRS Inist Pascal-Francis
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[PDF][PDF] Spinal muscular atrophy: mechanisms and therapeutic strategies

CL Lorson, H Rindt, M Shababi - Human Molecular Genetics, 2010 - Citeseer
Spinal muscular atrophy (SMA) is an autosomal recessive neurodegenerative disorder and
a leading genetic cause of infantile mortality. SMA is caused by mutation or deletion of …

Spinal muscular atrophy: mechanisms and therapeutic strategies.

CL Lorson, H Rindt, M Shababi - Human Molecular Genetics, 2010 - europepmc.org
Spinal muscular atrophy (SMA) is an autosomal recessive neurodegenerative disorder and
a leading genetic cause of infantile mortality. SMA is caused by mutation or deletion of …