Targeted gene addition at the CX3CR1 locus of human HSPCs improves their ability to repopulate the myeloid CNS compartment and drives lineage specific and …

A Biffi, A Montepeloso, D Mattioli, D Pellin, M Peviani… - 2023 - researchsquare.com
Transplantation of engineered hematopoietic stem and progenitor cells (HSPCs) showed
curative potential in patients affected by neurometabolic diseases treated in early stage …
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Targeted gene addition at the CX3CR1 locus of human HSPCs improves their ability to repopulate the myeloid CNS compartment and drives lineage specific and …

A Biffi, A Montepeloso, D Mattioli, D Pellin, M Peviani… - 2023 - europepmc.org
Transplantation of engineered hematopoietic stem and progenitor cells (HSPCs) showed
curative potential in patients affected by neurometabolic diseases treated in early stage …