[HTML][HTML] One drug to treat many diseases: unlocking the economic trap of rare diseases

K Pierzynowska, T Kamińska, G Węgrzyn - Metabolic Brain Disease, 2020 - Springer
There are two major problems with the development of therapies for rare diseases. First,
among over 7000 such diseases, the vast majority are caused by genetic defects and/or …

[PDF][PDF] One drug to treat many diseases: unlocking the economic trap of rare diseases

K Pierzynowska, T Kamińska, G Węgrzyn - 2020 - researchgate.net
There are two major problems with the development of therapies for rare diseases. First,
among over 7000 such diseases, the vast majority are caused by genetic defects and/or …

One drug to treat many diseases: unlocking the economic trap of rare diseases

K Pierzynowska, T Kamińska… - Metabolic brain …, 2020 - pubmed.ncbi.nlm.nih.gov
There are two major problems with the development of therapies for rare diseases. First,
among over 7000 such diseases, the vast majority are caused by genetic defects and/or …

[PDF][PDF] One drug to treat many diseases: unlocking the economic trap of rare diseases

K Pierzynowska, T Kamińska, G Węgrzyn - Metabolic Brain Disease, 2020 - d-nb.info
There are two major problems with the development of therapies for rare diseases. First,
among over 7000 such diseases, the vast majority are caused by genetic defects and/or …

One drug to treat many diseases: unlocking the economic trap of rare diseases.

K Pierzynowska, T Kamińska, G Węgrzyn - Metabolic Brain Disease, 2020 - europepmc.org
There are two major problems with the development of therapies for rare diseases. First,
among over 7000 such diseases, the vast majority are caused by genetic defects and/or …

One drug to treat many diseases: unlocking the economic trap of rare diseases

P Karolina, K Teresa, W Grzegorz - Metabolic Brain Disease, 2020 - search.proquest.com
There are two major problems with the development of therapies for rare diseases. First,
among over 7000 such diseases, the vast majority are caused by genetic defects and/or …

[PDF][PDF] One drug to treat many diseases: unlocking the economic trap of rare diseases

K Pierzynowska, T Kamińska… - Metabolic Brain …, 2020 - scholar.archive.org
There are two major problems with the development of therapies for rare diseases. First,
among over 7000 such diseases, the vast majority are caused by genetic defects and/or …

[HTML][HTML] One drug to treat many diseases: unlocking the economic trap of rare diseases

K Pierzynowska, T Kamińska… - Metabolic Brain Disease, 2020 - ncbi.nlm.nih.gov
There are two major problems with the development of therapies for rare diseases. First,
among over 7000 such diseases, the vast majority are caused by genetic defects and/or …

One drug to treat many diseases: unlocking the economic trap of rare diseases.

K Pierzynowska, T Kamińska… - Metabolic Brain …, 2020 - search.ebscohost.com
There are two major problems with the development of therapies for rare diseases. First,
among over 7000 such diseases, the vast majority are caused by genetic defects and/or …

One drug to treat many diseases: unlocking the economic trap of rare diseases

K Pierzynowska, T Kamińska… - Metabolic Brain …, 2020 - repozytorium.bg.ug.edu.pl
There are two major problems with the development of therapies for rare diseases. First,
among over 7000 such diseases, the vast majority are caused by genetic defects and/or …