… This review covers the recent progress in the development of genetic approaches to therapy
for DMD patients which target the basic defect rather than pharmacological approaches …

… Emerging therapeutic approaches include gene transfer therapy using adeno-associated
virus (AAV) … the current therapies used to treat DMD and explores the therapies currently being …

… , dystrophin levels, and timed exercises. The focus of this paper will be to report on current
and emerging therapies, with … therapy and benefit may be achieved in this orphan population. …

… of therapeutic approaches from untargeted drugs to new signaling and gene therapy
approaches with translational potential, and discuss current gaps in clinical trial readiness. …

… These forms of muscular dystrophy feature both skeletal muscle wasting … of muscular
dystrophy is Duchenne muscular dystrophy (DMD), which arises due to mutations in the dystrophin …

… therapies are facing on the road to translation, and discuss possible solutions and future
directions … the various genetic approaches that have been developed for FSHD therapy, discuss …

… different approaches … current development of gene therapy and focus on NMDs that are
available in published reports, including Duchenne Muscular Dystrophy (DMD), Becker muscular …

… This review discusses drugs already approved, as well as development progress made
in recent years by therapeutic strategies. Information on clinical trials conducted in the DMD …

… In this review, we discuss the existing cell therapy research, especially stem cell-based, which
… current methods of hPSCs myogenic commitment/differentiation, and describe the current …

… some of the latest developments in DMD gene therapy. Importantly, a … future directions of
DMD gene therapy. These insightful discussions have significant implications for gene therapy …