[HTML][HTML] Adeno-associated virus (AAV)-mediated gene therapy for Duchenne muscular dystrophy: the issue of transgene persistence

A Manini, E Abati, A Nuredini, S Corti… - Frontiers in …, 2022 - frontiersin.org
Duchenne muscular dystrophy (DMD) is an X-linked recessive, infancy-onset
neuromuscular disorder characterized by progressive muscle weakness and atrophy …

Adeno-Associated Virus (AAV)-mediated gene therapy for Duchenne muscular dystrophy: the issue of transgene persistence

A Manini, E Abati, A Nuredini, S Corti… - FRONTIERS IN …, 2022 - air.unimi.it
Duchenne muscular dystrophy (DMD) is an X-linked recessive, infancy-onset
neuromuscular disorder characterized by progressive muscle weakness and atrophy …

Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence.

A Manini, E Abati, A Nuredini, S Corti… - Frontiers in …, 2022 - europepmc.org
Duchenne muscular dystrophy (DMD) is an X-linked recessive, infancy-onset
neuromuscular disorder characterized by progressive muscle weakness and atrophy …

Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence

A Manini, E Abati, A Nuredini, S Corti… - Frontiers in …, 2022 - pubmed.ncbi.nlm.nih.gov
Duchenne muscular dystrophy (DMD) is an X-linked recessive, infancy-onset
neuromuscular disorder characterized by progressive muscle weakness and atrophy …

[HTML][HTML] Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence

A Manini, E Abati, A Nuredini, S Corti… - Frontiers in …, 2021 - ncbi.nlm.nih.gov
Duchenne muscular dystrophy (DMD) is an X-linked recessive, infancy-onset
neuromuscular disorder characterized by progressive muscle weakness and atrophy …

[PDF][PDF] Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence

A Manini, E Abati, A Nuredini, S Corti… - Front. Neurol. 12: 814174 …, 2022 - air.unimi.it
Duchenne muscular dystrophy (DMD) is an X-linked recessive, infancy-onset
neuromuscular disorder characterized by progressive muscle weakness and atrophy …

Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence.

A Manini, E Abati, A Nuredini, S Corti… - Frontiers in …, 2022 - europepmc.org
Duchenne muscular dystrophy (DMD) is an X-linked recessive, infancy-onset
neuromuscular disorder characterized by progressive muscle weakness and atrophy …