Effect of different corticosteroid dosing regimens on clinical outcomes in boys with Duchenne muscular dystrophy: a randomized clinical trial

M Guglieri, K Bushby, MP McDermott, KA Hart, R Tawil… - Jama, 2022 - jamanetwork.com
Importance Corticosteroids improve strength and function in boys with Duchenne muscular
dystrophy. However, there is uncertainty regarding the optimum regimen and dosage …

Developing standardized corticosteroid treatment for Duchenne muscular dystrophy

M Guglieri, K Bushby, MP McDermott, KA Hart… - Contemporary clinical …, 2017 - Elsevier
Despite corticosteroids being the only treatment documented to improve strength and
function in boys with Duchenne muscular dystrophy (DMD) corticosteroid prescription is …

Long-term outcome of interdisciplinary management of patients with Duchenne muscular dystrophy receiving daily glucocorticoid treatment

BL Wong, I Rybalsky, KC Shellenbarger, C Tian… - The Journal of …, 2017 - Elsevier
Objective To evaluate clinical outcomes and steroid side effects in a cohort of patients with
Duchenne muscular dystrophy (DMD) treated with long-term daily glucocorticoid therapy …

Change in natural history of Duchenne muscular dystrophy with long-term corticosteroid treatment: implications for management

RT Moxley III, S Pandya, E Ciafaloni… - Journal of child …, 2010 - journals.sagepub.com
In 2005, the American Academy of Neurology and the Child Neurology Society published a
practice parameter, based primarily on studies that involved 6 to 18 months of treatment …

Deflazacort vs prednisone treatment for Duchenne muscular dystrophy: a meta‐analysis of disease progression rates in recent multicenter clinical trials

CM McDonald, G Sajeev, Z Yao, E McDonnell… - Muscle & …, 2020 - Wiley Online Library
Introduction In this study we characterized disease progression over 48 weeks among boys
receiving deflazacort vs prednisone/prednisolone placebo arm treatment in two recent …

Corticosteroids in Duchenne muscular dystrophy: a reappraisal

BLY Wong, C Christopher - Journal of child neurology, 2002 - journals.sagepub.com
Duchenne muscular dystrophy is the most common and most severe form of childhood
muscular dystrophies, resulting in early loss of ambulation between the ages of 7 and 13 …

Practice parameter: corticosteroid treatment of Duchenne dystrophy: report of the Quality Standards Subcommittee of the American Academy of Neurology and the …

RT Moxley III, S Ashwal, S Pandya, A Connolly… - Neurology, 2005 - AAN Enterprises
Background: The Quality Standards Subcommittee of the American Academy of Neurology
and the Practice Committee of the Child Neurology Society develop practice parameters as …

Early corticosteroid treatment in 4 Duchenne muscular dystrophy patients: 14‐year follow‐up

L Merlini, M Gennari, E Malaspina, I Cecconi… - Muscle & …, 2012 - Wiley Online Library
Introduction: Corticosteroid treatment is the standard of care in Duchenne muscular
dystrophy (DMD), but the optimal age to initiate treatment and dosage pattern remain a …

Practice guideline update summary: Corticosteroid treatment of Duchenne muscular dystrophy: Report of the Guideline Development Subcommittee of the American …

D Gloss, RT Moxley III, S Ashwal, M Oskoui - Neurology, 2016 - AAN Enterprises
Objective: To update the 2005 American Academy of Neurology (AAN) guideline on
corticosteroid treatment of Duchenne muscular dystrophy (DMD). Methods: We …

High dose weekly oral prednisone improves strength in boys with Duchenne muscular dystrophy

AM Connolly, J Schierbecker, R Renna… - Neuromuscular …, 2002 - Elsevier
Daily prednisone improves strength in boys with Duchenne muscular dystrophy, but side
effects are almost universal. We used a different dosing regimen of prednisone to determine …