Therapeutic exon skipping through a CRISPR-guided cytidine deaminase rescues dystrophic cardiomyopathy in vivo

J Li, K Wang, Y Zhang, T Qi, J Yuan, L Zhang, H Qiu… - Circulation, 2021 - Am Heart Assoc
Background: Loss of dystrophin protein causes Duchenne muscular dystrophy (DMD),
characterized by progressive degeneration of cardiac and skeletal muscles, and mortality in …

Therapeutic Exon Skipping Through a CRISPR-Guided Cytidine Deaminase Rescues Dystrophic Cardiomyopathy in Vivo

J Li, K Wang, Y Zhang, T Qi, J Yuan, L Zhang, H Qiu… - Circulation, 2021 - Am Heart Assoc
Background: Loss of dystrophin protein causes Duchenne muscular dystrophy (DMD),
characterized by progressive degeneration of cardiac and skeletal muscles, and mortality in …

[PDF][PDF] Therapeutic Exon Skipping Through a CRISPR-Guided Cytidine Deaminase Rescues Dystrophic Cardiomyopathy in Vivo

J Li, K Wang, Y Zhang, T Qi, J Yuan, L Zhang, H Qiu… - Circulation, 2021 - researchgate.net
BACKGROUND: Loss of dystrophin protein causes Duchenne muscular dystrophy (DMD),
characterized by progressive degeneration of cardiac and skeletal muscles, and mortality in …

Therapeutic Exon Skipping Through a CRISPR-Guided Cytidine Deaminase Rescues Dystrophic Cardiomyopathy in Vivo

J Li, K Wang, Y Zhang, T Qi, J Yuan, L Zhang… - …, 2021 - pubmed.ncbi.nlm.nih.gov
Background Loss of dystrophin protein causes Duchenne muscular dystrophy (DMD),
characterized by progressive degeneration of cardiac and skeletal muscles, and mortality in …

Therapeutic Exon Skipping via a CRISPR-guided Cytidine Deaminase Rescues Dystrophic Cardiomyopathy In Vivo.

J Li, K Wang, Y Zhang, T Qi, J Yuan, L Zhang, H Qiu… - Circulation, 2021 - europepmc.org
Background: Loss of dystrophin protein causes Duchenne muscular dystrophy (DMD),
characterized by progressive degeneration of cardiac and skeletal muscles, and mortality in …