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[HTML][HTML] Hematopoietic stem cell transplantation in mucopolysaccharidosis type IIIA: A case description and comparison with a genotype-matched control group

AF Köhn, L Grigull, M du Moulin, S Kabisch… - Molecular Genetics and …, 2020 - Elsevier
Abstract Background Mucopolysaccharidosis type IIIA (MPS IIIA, Sanfilippo A syndrome) is a
chronic progressive neurodegenerative storage disorder caused by a deficiency of …
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[HTML][HTML] Hematopoietic stem cell transplantation in mucopolysaccharidosis type IIIA: A case description and comparison with a genotype-matched control group

AF Köhn, L Grigull, M du Moulin, S Kabisch… - Molecular Genetics …, 2020 - ncbi.nlm.nih.gov
Background Mucopolysaccharidosis type IIIA (MPS IIIA, Sanfilippo A syndrome) is a chronic
progressive neurodegenerative storage disorder caused by a deficiency of lysosomal …

Hematopoietic stem cell transplantation in mucopolysaccharidosis type IIIA: A case description and comparison with a genotype-matched control group

AF Köhn, L Grigull, M du Moulin, S Kabisch, L Ammer… - 2020 - agris.fao.org
Background: Mucopolysaccharidosis type IIIA (MPS IIIA, Sanfilippo A syndrome) is a chronic
progressive neurodegenerative storage disorder caused by a deficiency of lysosomal …

Hematopoietic stem cell transplantation in mucopolysaccharidosis type IIIA: A case description and comparison with a genotype-matched control group.

AF Köhn, L Grigull, M du Moulin, S Kabisch… - Molecular Genetics …, 2020 - europepmc.org
Background Mucopolysaccharidosis type IIIA (MPS IIIA, Sanfilippo A syndrome) is a chronic
progressive neurodegenerative storage disorder caused by a deficiency of lysosomal …

Hematopoietic stem cell transplantation in mucopolysaccharidosis type IIIA: A case description and comparison with a genotype-matched control group

AF Köhn, L Grigull, M du Moulin… - Molecular genetics …, 2020 - pubmed.ncbi.nlm.nih.gov
Background Mucopolysaccharidosis type IIIA (MPS IIIA, Sanfilippo A syndrome) is a chronic
progressive neurodegenerative storage disorder caused by a deficiency of lysosomal …