Striking a balance in Fabry disease research: Mitigating the statistical dilemma arising from small sample size and modest event frequency in rare disorders

B Bernhard, C Gräni - International …, 2023 - internationaljournalofcardiology.com
Cardiac involvement is a common and significant source of morbidity and mortality in Fabry
disease (FD). The severity of cardiac involvement can vary widely among patients, making it …

[PDF][PDF] Striking a balance in Fabry disease research: Mitigating the statistical dilemma arising from small sample sizes and modest event frequencies in rare disorders.

B Bernhard, C Gräni - International journal of cardiology, 2023 - boris.unibe.ch
Cardiac involvement is a common and significant source of morbidity and mortality in Fabry
disease (FD). The severity of cardiac involvement can vary widely among patients, making it …

[引用][C] Striking a balance in Fabry disease research: Mitigating the statistical dilemma arising from small sample size and modest event frequency in rare disorders

B Bernhard, C Gräni - International journal of cardiology, 2023 - pubmed.ncbi.nlm.nih.gov
Striking a balance in Fabry disease research: Mitigating the statistical dilemma arising from
small sample size and modest event frequency in rare disorders Striking a balance in Fabry …

[引用][C] Striking a balance in Fabry disease research: Mitigating the statistical dilemma arising from small sample sizes and modest event frequencies in rare disorders.

B Bernhard, C Gräni - International Journal of Cardiology, 2023 - europepmc.org
Striking a balance in Fabry disease research: Mitigating the statistical dilemma arising from
small sample sizes and modest event frequencies in rare disorders. - Abstract - Europe PMC …