Antisense-mediated modulation of splicing: therapeutic implications for Duchenne muscular dystrophy

A Aartsma-Rus - RNA biology, 2010 - Taylor & Francis
While disruption of alternative splicing underlies many diseases, modulation of splicing
using antisense oligonucleotides (AONs) can have therapeutic implications. The most …

[引用][C] Antisense-mediated modulation of splicing: Therapeutic implications for Duchenne muscular dystrophy

A Aartsma-Rus - RNA Biology, 2010 - cir.nii.ac.jp
Antisense-mediated modulation of splicing: Therapeutic implications for Duchenne muscular
dystrophy | CiNii Research CiNii 国立情報学研究所 学術情報ナビゲータ[サイニィ] 詳細へ移動 検索 …

Antisense-mediated modulation of splicing Therapeutic implications for duchenne muscular dystrophy

A Aartsma-Rus - RNA Biology, 2010 - scholarlypublications …
While disruption of alternative splicing underlies many diseases, modulation of splicing
using antisense oligonucleotides (AONs) can have therapeutic implications. The most …

Antisense-mediated modulation of splicing: therapeutic implications for Duchenne muscular dystrophy

A Aartsma-Rus - RNA biology, 2010 - pubmed.ncbi.nlm.nih.gov
While disruption of alternative splicing underlies many diseases, modulation of splicing
using antisense oligonucleotides (AONs) can have therapeutic implications. The most …

Antisense-mediated modulation of splicing: therapeutic implications for Duchenne muscular dystrophy.

A Aartsma-Rus - RNA Biology, 2010 - europepmc.org
While disruption of alternative splicing underlies many diseases, modulation of splicing
using antisense oligonucleotides (AONs) can have therapeutic implications. The most …

[引用][C] Antisense-mediated modulation of splicing: Therapeutic implications for Duchenne muscular dystrophy

A Aartsma-Rus - 2010