[HTML][HTML] Duchenne 型肌营养不良基因治疗研究进展
董奇超 - Chinese Journal of Contemporary Pediatrics, 2018 - ncbi.nlm.nih.gov
Abstract Duchenne 型肌营养不良（ DMD） 是由编码抗肌萎缩蛋白的DMD 基因突变导致的X
连锁隐性遗传病。 它的特点是进行性肌无力和因缺乏抗肌萎缩蛋白而导致的骨骼肌和心肌退化 …
连锁隐性遗传病。 它的特点是进行性肌无力和因缺乏抗肌萎缩蛋白而导致的骨骼肌和心肌退化 …
A review of gene therapy for Duchenne muscular dystrophy
QC Dong, HM Chen, X Jin - Zhongguo Dang dai er ke za zhi …, 2018 - europepmc.org
Abstract Duchenne 型肌营养不良 (DMD) 是由编码抗肌萎缩蛋白的 DMD 基因突变导致的 X
连锁隐性遗传病. 它的特点是进行性肌无力和因缺乏抗肌萎缩蛋白而导致的骨骼肌和心肌退化 …
连锁隐性遗传病. 它的特点是进行性肌无力和因缺乏抗肌萎缩蛋白而导致的骨骼肌和心肌退化 …
Research progress of therapeutic methods to restore dystrophin expression in Duchenne muscular dystrophy
X WU, L YU, M LIU, Q FANG - Chinese Journal of Neurology, 2022 - pesquisa.bvsalud.org
Duchenne muscular dystrophy (DMD) is a serious and progressive hereditary muscle
disease. The DMD gene mutation on the X chromosome causes the loss of dystrophin …
disease. The DMD gene mutation on the X chromosome causes the loss of dystrophin …
Therapy for Duchenne muscular dystrophy: renewed optimism from genetic approaches
RJ Fairclough, MJ Wood, KE Davies - Nature Reviews Genetics, 2013 - nature.com
Duchenne muscular dystrophy (DMD) is a devastating progressive disease for which there
is currently no effective treatment except palliative therapy. There are several promising …
is currently no effective treatment except palliative therapy. There are several promising …
Genetic correction strategies for Duchenne Muscular Dystrophy and their impact on the heart
JR Johnston, EM McNally - Progress in pediatric cardiology, 2021 - Elsevier
Background Duchenne muscular dystrophy (DMD) is an X-linked recessive disorder with
early childhood onset characterized by profound loss of muscle strength and associated …
early childhood onset characterized by profound loss of muscle strength and associated …
Duchenne muscular dystrophy: Current treatment and emerging exon skipping and gene therapy approach
G Patterson, H Conner, M Groneman, C Blavo… - European Journal of …, 2023 - Elsevier
Duchenne muscular dystrophy (DMD) is an X-linked recessive neuromuscular disorder that
causes debilitating muscle weakness and atrophy due to a loss of the dystrophin protein …
causes debilitating muscle weakness and atrophy due to a loss of the dystrophin protein …
Genetic therapeutic approaches for Duchenne muscular dystrophy
H Foster, L Popplewell, G Dickson - Human gene therapy, 2012 - liebertpub.com
Despite an expansive wealth of research following the discovery of the DMD gene 25 years
ago, there is still no curative treatment for Duchenne muscular dystrophy. However, there …
ago, there is still no curative treatment for Duchenne muscular dystrophy. However, there …