… Preclinical CRISPR/Cas9 therapy in inherited disease models presented in the … inherited
disease treatments. This could provide simplicity and precision in mammalian genome editing. …

… the gene editing landscape. This newcomer has broadened the potential therapeutic applications
of gene editing to correct inherited diseases… gene editing strategies to correct inherited …

… to inactivation of the gene-causing disease. Genome editing has advanced at an exceptionally
rapid rate and CRISPR/Cas system has speeded up the genome editing revolution. This …

… of CRISPR-Cas9-based gene editing and will focus on the … gene editing trials. In addition,
the review will summarize the current barriers to the wider use of CRISPR-Cas9 gene editing …

… This study also highlighted that use of knock-in into a safe harbour is a promising strategy
for long-term correction of inherited diseases [81]. In another recent study, CRISPR was used …

… progress in treating inherited genetic disorders that remain … of various programmable
genome editing systems with their … inherited diseases in the clinic, including sickle cell disease (…

… genome editing offers a potential link in not only investigating the pathogenicity of these
primary genetic … Key phenotypic features of inherited cardiac diseases that are seen in patients …

… with genetic conditions are crucial to include in public dialogue around developing gene
editing … This qualitative study sought to characterize the attitudes of people with inherited retinal …

… Gene augmentation and genome editing are promising strategies for the treatment of
monogenic inherited retinal diseases. Although gene augmentation treatments are commercially …

… genome editing tools has been used in various fields to further our knowledge on the
pathophysiology of certain diseases … diverse applications of genome editing in the understanding …