Duchenne muscular dystrophy (DMD) is a severe, progressive, muscle-wasting disease,
characterized by progressive deterioration of skeletal muscle that causes rapid loss of …

GSK/Prosensa's failure doesn't represent undiluted good news given that the utility of exon
skipping is in question and the challenge of designing a study to demonstrate clinical …

Duchenne muscular dystrophy (DMD) is an X-linked progressive muscle-wasting disorder
that is caused by a lack of functional dystrophin, a cytoplasmic protein necessary for the …

Duchenne muscular dystrophy (DMD) is the most common childhood muscular dystrophy
and results from mutations in the dystrophin gene. Currently no treatment is available for this …

Duchenne muscular dystrophy (DMD) is an X-linked condition caused by a deficiency of
functional dystrophin protein. Patients experience progressive muscle weakness …

Neuromuscular disorders encompass a heterogeneous group of conditions that impair the
function of muscles, motor neurons, peripheral nerves, and neuromuscular junctions. Being …

Duchenne Muscular Dystrophy (DMD) is one of the most prevalent genetic disorders of
childhood for which there is no cure. This authoritative guide provides a clear overview of …

Duchenne muscular dystrophy (DMD) is a genetic, lethal, muscle disorder caused by the
loss of the muscle protein, dystrophin, leading to progressive loss of muscle fibers and …

Despite the full cloning of the Dystrophin cDNA 35 years ago, no effective treatment exists
for the Duchenne Muscular Dystrophy (DMD) patients who have a mutation in this gene …

Duchenne muscular dystrophy (DMD) is an X-linked recessive disorder caused by defects in
the dystrophin gene. Patients exhibit progressive muscle degeneration, generally begin …