The development of new therapeutic agents for the treatment of Duchenne muscular
dystrophy has put a focus on defining outcome measures most sensitive to capture treatment …

Duchenne muscular dystrophy (DMD) is a progressive genetic muscle disease. Quantitative
muscle ultrasound (US), muscle MRI, and functional tools are important to delineate …

While the number of new treatment options tested in patients with Duchenne muscular
dystrophy (DMD) is increasing, there is still no defining of the most reliable assessments …

Background The aim of this study was to perform a longitudinal assessment using
Quantitative Muscle Testing (QMT) in a cohort of ambulant boys affected by Duchenne …

The recent development of therapeutic approaches for Duchenne muscular dystrophy
(DMD) has highlighted the need to identify clinical outcome measures for planned efficacy …

Purpose To validate a multicenter protocol that examines lower extremity skeletal muscles of
children with Duchenne muscular dystrophy (DMD) by using magnetic resonance (MR) …

Introduction: Tests of ambulatory function are common clinical trial endpoints in Duchenne
muscular dystrophy (DMD). Using these tests, the ImagingDMD study has generated a large …

There is a pressing need for biomarkers and outcomes that can be used across disease
stages in Duchenne muscular dystrophy (DMD), to facilitate the inclusion of a wider range of …

Aim To develop a patient‐reported outcome measure (PROM) assessing upper limb function
related to activities of daily living (ADL) that cannot be observed in a clinical setting …

Introduction The definition of reliable outcome measures is of increasing interest in patients
with Duchenne muscular dystrophy (DMD). Methods In this retrospective study, we analyzed …