Introduction Duchenne muscular dystrophy (DMD) is the most common myopathy in
children, with a worldwide prevalence of approximately 0.5 cases per 10 000 male births. It …

Background Several studies on clinical practice for Duchenne muscular dystrophy (DMD)
have been conducted in Western countries. However, there have been only a few similar …

Muscular dystrophies are a clinically and genetically heterogeneous group of skeletal
muscle-wasting diseases. Even for experts in the field of neuromuscular diseases, it is …

Background: Recent short-term clinical trials in patients with Duchenne Muscular Dystrophy
(DMD) have indicated greater disease variability in terms of progression than expected. In …

The field of translational research in Duchenne muscular dystrophy (DMD) has been
transformed in the last decade by a number of therapeutic targets, mostly studied in …

Introduction Duchenne muscular dystrophy (DMD) is a devastatingly severe genetic muscle
disease characterized by childhood-onset muscle weakness, leading to loss of motor …

Duchenne muscular dystrophy (DMD) is the most common and severe childhood muscular
dystrophy, resulting in progressive muscle weakness and wasting, disability and decreased …

Duchenne muscular dystrophy is a genetically determined X-linked disease and the most
common, progressive pediatric muscle disorder. For decades, research has been conducted …

Opinion statement The main goal in the treatment of Duchenne muscular dystrophy (DMD) is
to maintain ambulation for as long as possible and to anticipate and manage the associated …

Abstract Introduction/Aims Prognostic factors in Duchenne muscular dystrophy (DMD)
predict the disease course and may help individualize patient care. The aim was to …