Pediatric neuromuscular disorders comprise a large variety of disorders that can be
classified based on their neuroanatomical localization, patterns of weakness, and laboratory …

Background: Evidence on the long-term efficacy of steroids in Duchenne muscular dystrophy
(DMD) after loss of ambulation is limited. Objective: Characterize and compare disease …

Introduction: Duchenne muscular dystrophy (DMD) is the most common, severe childhood
form of muscular dystrophy. Treatment is limited to glucocorticoids that have the benefit of …

Background: As new gene-related treatment options for Duchenne muscular dystrophy
(DMD) are being developed, precise information about the patients' genetic diagnosis and …

In the last few decades, there have been considerable improvements in the diagnosis and
care of Duchenne muscular dystrophy (DMD), the most common childhood muscular …

Duchenne muscular dystrophy (DMD) is an X-linked myopathy resulting in progressive
weakness and wasting of all the striated muscles including the respiratory muscles. The …

Background Duchenne muscular dystrophy is a rare X-linked progressive disease
characterised by loss of ambulation at about age 10 years, with death in early adulthood due …

Duchenne muscular dystrophy is a severe, progressive, muscle-wasting disease that leads
to difficulties with movement and, eventually, to the need for assisted ventilation and …

Duchenne muscular dystrophy is a severe, progressive, muscle-wasting disease that leads
to difficulties with movement and, eventually, to the need for assisted ventilation and …

Despite all the advances in diagnosis and management of Duchenne muscular dystrophy
over the past 50 years, the average age at diagnosis in most countries in the world around is …