Duchenne muscular dystrophy (DMD) is a devastating disease affecting about 1 out of 5000
male births and caused by mutations in the dystrophin gene. Genome editing has the …

Duchenne muscular dystrophy (DMD) is a severe, progressive muscle disease caused by
mutations in the dystrophin gene. The majority of DMD mutations are deletions that …

Duchenne muscular dystrophy (DMD), one of the most common neuromuscular disorders of
children, is caused by the absence of dystrophin protein in striated muscle. Deletions of …

CRISPR/Cas9-mediated genome editing holds clinical potential for treating genetic
diseases, such as Duchenne muscular dystrophy (DMD), which is caused by mutations in …

Duchenne muscular dystrophy (DMD) is an inherited X-linked disease caused by mutations
in the gene encoding dystrophin, a protein required for muscle fiber integrity. DMD is …

Rationale: Duchenne muscular dystrophy is a severe inherited form of muscular dystrophy
caused by mutations in the reading frame of the dystrophin gene disrupting its protein …

Duchenne muscular dystrophy (DMD) is a degenerative muscle disease caused by genetic
mutations that lead to the disruption of dystrophin in muscle fibers. There is no curative …

Duchenne muscular dystrophy (DMD) is a lethal neuromuscular disease caused by
mutations in the dystrophin gene (DMD). Previously, we applied CRISPR-Cas9–mediated …

Duchenne muscular dystrophy is one of the most common inherited genetic diseases and is
caused by mutations to the DMD gene that encodes the dystrophin protein. Recent …

Frame-disrupting mutations in the DMD gene, encoding dystrophin, compromise myofiber
integrity and drive muscle deterioration in Duchenne muscular dystrophy (DMD). Removing …