Duchenne muscular dystrophy (DMD) is a lethal neuromuscular disorder caused by loss of
dystrophin. Several therapeutic modalities are currently in clinical trials but none will achieve …

Duchenne muscular dystrophy (DMD) is a severe muscle-wasting disorder for which there is
currently no effective treatment. This disorder is caused by mutations or deletions in the …

Duchenne muscular dystrophy (DMD), a severe X-linked genetic disease affecting one in
3500 boys, is the most common myopathy in children. DMD is due to a lack of dystrophin, a …

Duchenne muscular dystrophy (DMD) is a fatal disorder caused by absence of functional
dystrophin protein. Compensation in dystrophin‐deficient (mdx) mice may be achieved by …

Although the molecular defect causing Duchenne/Becker muscular dystrophy (DMD/BMD)
was identified nearly 20 years ago, the development of effective therapeutic strategies has …

Utrophin is an autosomal paralogue of dystrophin, a protein whose deficit causes Duchenne
and Becker muscular dystrophies (DMD/BMD). Utrophin is naturally overexpressed at the …

Duchenne muscular dystrophy (DMD) is an inherited, severe muscle wasting disease
caused by the loss of the cytoskeletal protein, dystrophin. Patients usually die in their late …

Duchenne Muscular Dystrophy (DMD) is a devastating, progressive muscle wasting disease
for which there is currently no effective treatment. DMD is caused by mutations in the …

Duchenne muscular dystrophy is an X-linked recessive muscle wasting disease caused by
the absence of the muscle cytoskeletal protein, dystrophin. Dystrophin is a member of the …

Introduction: Duchenne muscular dystrophy (DMD) is a devastating genetic muscle wasting
disease caused by mutations in the DMD gene that in turn lead to an absence of dystrophin …