[HTML][HTML] Duchenne muscular dystrophy

EJ Annexstad, I Lund-Petersen… - Tidsskrift for Den norske …, 2014 - tidsskriftet.no
BACKGROUND Duchenne muscular dystrophy is one of the most severe muscle diseases
to affect children. In the last twenty years, treatments have been established that have …

Recent developments in the management of Duchenne muscular dystrophy

M Guglieri, K Bushby - Paediatrics and Child Health, 2015 - Elsevier
Duchenne muscular dystrophy (DMD) is the most common severe heritable muscle disorder
of childhood. Affected boys show first symptoms around the age of 2–5 years with …

[PDF][PDF] State of the art advances in Duchenne muscular dystrophy

H Van Ruiten, K Bushby, M Guglieri - EMJ, 2017 - emjreviews.com
Duchenne muscular dystrophy (DMD) is a severe and fatal muscle condition affecting young
children. Without interventions, affected boys lose the ability to walk independently by the …

Recent developments in the management of Duchenne muscular dystrophy

M Guglieri, K Bushby - Paediatrics and Child Health, 2011 - Elsevier
Duchenne muscular dystrophy (DMD) is the most common paediatric muscle condition.
Affected boys show first symptoms around the age of 2–5 years with progressive muscle …

Treatment options for Duchenne muscular dystrophy

E Ciafaloni, RT Moxley - Current treatment options in neurology, 2008 - Springer
Opinion statement The main goal in the treatment of Duchenne muscular dystrophy (DMD) is
to maintain ambulation for as long as possible and to anticipate and manage the associated …

Current and emerging treatment strategies for Duchenne muscular dystrophy

JK Mah - Neuropsychiatric disease and treatment, 2016 - Taylor & Francis
Duchenne muscular dystrophy (DMD) is the most common form of muscular dystrophy in
childhood. It is caused by mutations of the DMD gene, leading to progressive muscle …

[HTML][HTML] Duchenne muscular dystrophy: Case report and review

R Sinha, S Sarkar, T Khaitan… - Journal of family medicine …, 2017 - journals.lww.com
Muscular dystrophies are a clinically and heterogeneous group of disorders that all share
clinical characteristics of progressive muscular weakness. Duchenne muscular dystrophy …

[HTML][HTML] The burden, epidemiology, costs and treatment for Duchenne muscular dystrophy: an evidence review

S Ryder, RM Leadley, N Armstrong… - Orphanet journal of rare …, 2017 - Springer
Abstract Background Duchenne Muscular Dystrophy (DMD) is a rapidly progressive, lethal
neuromuscular disorder, present from birth, which occurs almost exclusively in males. We …

[HTML][HTML] European cross-sectional survey of current care practices for Duchenne muscular dystrophy reveals regional and age-dependent differences

J Vry, K Gramsch, S Rodger… - Journal of …, 2016 - content.iospress.com
Background: Publication of comprehensive clinical care guidelines for Duchenne muscular
dystrophy (DMD) in 2010 was a milestone for DMD patient management. Our CARE-NMD …

Duchenne muscular dystrophy.

T Metules - RN, 2002 - europepmc.org
It's the most common form of muscular dystrophy to present in children, and it often takes
their life in young adulthood. But thanks to a better understanding of this disease, these …