Drug discovery approaches for rare neuromuscular diseases

GM Wynne, AJ Russell - 2014 - books.rsc.org
Rare neuromuscular diseases encompass many diverse and debilitating musculoskeletal
disorders, ranging from ultra-orphan conditions that affect only a few families, to the so …

Drug Discovery Approaches for Rare Neuromuscular Diseases

GM Wynne, AJ Russell - 2014 - books.rsc.org
Rare neuromuscular diseases encompass many diverse and debilitating disorders, ranging
from ultra-orphan conditions such as various forms of autosomal dominant limb-girdle …

Drug Discovery Approaches for Rare Neuromuscular Diseases

GM WYNNE, AJ RUSSELL - Orphan Drugs and Rare Diseases, 2014 - books.google.com
Rare neuromuscular diseases encompass many diverse and debilitating disorders, ranging
from ultra-orphan conditions such as various forms of autosomal dominant limb-girdle …

Drug Discovery Approaches for Rare Neuromuscular Diseases

GM WYNNE, AJ RUSSELL - Orphan Drugs and Rare Diseases, 2014 - books.google.com
Rare neuromuscular diseases encompass many diverse and debilitating disorders, ranging
from ultra-orphan conditions such as various forms of autosomal dominant limb-girdle …