An updated systematic review of studies mapping (or cross-walking) measures of health-related quality of life to generic preference-based measures to generate utility …

C Mukuria, D Rowen, S Harnan, A Rawdin… - … health economics and …, 2019 - Springer
Background Mapping is an increasingly common method used to predict instrument-specific
preference-based health-state utility values (HSUVs) from data obtained from another health …

'Mapping'health state utility values from non-preference-based measures: a systematic literature review in rare diseases

M Meregaglia, A Whittal, E Nicod, M Drummond - Pharmacoeconomics, 2020 - Springer
Background The use of patient-reported outcome measures (PROMs) to monitor the effects
of disease and treatment on patient symptomatology and daily life is increasing in rare …

Health-related quality of life in amyotrophic lateral sclerosis using EQ-5D-5L

QQ Wei, Y Hou, Y Chen, R Ou, B Cao, L Zhang… - Health and Quality of …, 2021 - Springer
Background The study aimed to appraise the health-related quality of life (HRQoL)
measured by the five-level EuroQol-5 dimensions (EQ-5D-5L) in amyotrophic lateral …

Health utilities and quality-adjusted life years for patients with amyotrophic lateral sclerosis receiving reldesemtiv or placebo in FORTITUDE-ALS

P Gebrehiwet, L Meng, SA Rudnicki… - Journal of medical …, 2023 - Taylor & Francis
Aims To estimate the health utilities and quality-adjusted life years (QALYs) in patients with
amyotrophic lateral sclerosis (ALS) receiving reldesemtiv versus placebo in FORTITUDE …

Estimating treatment effects on health utility scores for patients living with migraine: a post hoc analysis of the DELIVER trial

L Jönsson, SA Regnier, S Kymes, SF Awad… - Expert Review of …, 2023 - Taylor & Francis
Background This post hoc analysis aimed to estimate eptinezumab's therapeutic effect on
health utilities and determined to which extent monthly migraine days (MMDs) explain …

Generating EQ-5D-5L health utility scores from BASDAI and BASFI: a mapping study in patients with axial spondyloarthritis using longitudinal UK registry data

AR Neilson, GT Jones, GJ Macfarlane… - The European Journal of …, 2022 - Springer
Background Preference-based health-state utility values (HSUVs), such as the EuroQol five-
dimensional questionnaire (EQ-5D-5L), are needed to calculate quality-adjusted life-years …

[HTML][HTML] Mapping studies to estimate health-state utilities from nonpreference-based outcome measures: a systematic review on how repeated measurements are …

ASO Gonçalves, S Werdin, T Kurth, D Panteli - Value in Health, 2023 - Elsevier
Objectives Mapping algorithms are developed using data sets containing patient responses
to a preference-based questionnaire and another health-related quality-of-life questionnaire …

Health-Related Quality of Life in Adults With Classical Infratentorial Superficial Siderosis: A Cross-sectional Study

N Kharytaniuk, AA Mazaheri, M Pavlou, DJ Werring… - Neurology, 2022 - AAN Enterprises
Background and Objectives Infratentorial superficial siderosis (iSS) is a rare but disabling
neurologic condition characterized by progressive hearing loss and balance and mobility …

Medical therapies for amyotrophic lateral sclerosis-related respiratory decline: an appraisal of needs, opportunities and obstacles

C Young, S Pinto, J Grosskreutz… - … Lateral Sclerosis and …, 2022 - Taylor & Francis
A roundtable convened in July 2020 examined issues concerning respiratory support in
amyotrophic lateral sclerosis (ALS), with reference to the potential for an early-phase orally …

VOLUME VERSUS PRESSURE TARGETED NON-INVASIVE VENTILATION IN AMYOTROPHIC LATERAL SCLEROSIS (VOP ALS): study protocol for a randomised …

E Parkes, SW Hee, A Ali, J Shakespeare - 2024 - researchsquare.com
Amyotrophic lateral sclerosis (ALS) is a rare, idiopathic, progressive, neuromuscular
disease. The prevalence in England and Wales is between 4 and 5 cases per 100,000. A …