[HTML][HTML] A systematic review of moral reasons on orphan drug reimbursement

BM Zimmermann, J Eichinger… - Orphanet Journal of Rare …, 2021 - Springer
Background The number of market approvals of orphan medicinal products (OMPs) has
been increasing steadily in the last 3 decades. While OMPs can offer a unique chance for …

Orphan Drugs: Regulatory Framework, Market Positioning and Major Development Challenges and Strategies

IPF Amaral - 2016 - search.proquest.com
Orphan Drug is a pharmaceutical product aimed at a rare disease. In the world, there are
more than 6000 rare diseases; 80% of them are of genetic origin, and are often chronic and …