In vivo delivery of CRISPR-Cas9 genome editing components for therapeutic applications

K Huang, D Zapata, Y Tang, Y Teng, Y Li - Biomaterials, 2022 - Elsevier
Since its mechanism discovery in 2012 and the first application for mammalian genome
editing in 2013, CRISPR-Cas9 has revolutionized the genome engineering field and created …

Nanobiomaterial vectors for improving gene editing and gene therapy

SW Hu, T Ding, H Tang, H Guo, W Cui, Y Shu - Materials Today, 2023 - Elsevier
With the development of genome editing techniques, gene therapy is becoming a viable
option for the treatment of a variety of human diseases. Genome editing techniques mainly …

A duplex CRISPR-Cas9 ribonucleoprotein nanomedicine for colorectal cancer gene therapy

T Wan, Q Pan, C Liu, J Guo, B Li, X Yan, Y Cheng… - Nano Letters, 2021 - ACS Publications
Based on the high frequency of concurrent adenomatous polyposis coli (APC) and KRAS
mutations and their strong cooperative interaction in human colorectal cancer (CRC) …

Guanidyl-Rich Poly (β amino ester) s for Universal Functional Cytosolic protein delivery and clustered regularly interspaced short palindromic repeats (CRISPR) Cas9 …

X Wang, Y Li, X Wang, DM Sandoval, Z He, IL Sáez… - ACS …, 2023 - ACS Publications
Protein therapeutics are highly promising for complex disease treatment. However, the lack
of ideal delivery vectors impedes their clinical use, especially the carriers for in vivo delivery …

[HTML][HTML] CRISPR-Cas9 gene therapy for Duchenne muscular dystrophy

CH Mbakam, G Lamothe, G Tremblay, JP Tremblay - Neurotherapeutics, 2022 - Elsevier
Discovery of the CRISPR-Cas (clustered regularly interspaced short palindromic repeat,
CRISPR-associated) system a decade ago has opened new possibilities in the field of …

Recent advances in the delivery and applications of nonviral CRISPR/Cas9 gene editing

F Sinclair, AA Begum, CC Dai, I Toth… - Drug delivery and …, 2023 - Springer
The CRISPR (clustered regularly interspaced short palindromic repeats)/Cas9 genome
editing system has been a major technological breakthrough that has brought revolutionary …

Nucleic acid-based therapeutics for dermal wound healing

P Sharma, A Kumar, T Agarwal, AD Dey… - International Journal of …, 2022 - Elsevier
Non-healing wounds have long been the subject of scientific and clinical investigations.
Despite breakthroughs in understanding the biology of delayed wound healing, only limited …

3D macrocyclic structure boosted gene delivery: multi-cyclic poly (β-amino Ester) s from step growth polymerization

Y Li, X Wang, Z He, M Johnson… - Journal of the …, 2023 - ACS Publications
The topological structures of polymers play a critical role in determining their gene delivery
efficiency. Exploring novel polymeric structures as gene delivery vectors is thus of great …

Enhanced gene transfection efficacy and safety through granular hydrogel mediated gene delivery process

J Zhang, Z He, Y Li, Y Shen, G Wu, L Power, R Song… - Acta Biomaterialia, 2023 - Elsevier
Although gene therapy has made great achievements in both laboratory research and
clinical translation, there are still challenges such as limited control of drug …

Preclinical model for phenotypic correction of dystrophic epidermolysis bullosa by in vivo CRISPR-Cas9 delivery using adenoviral vectors

M García, J Bonafont, J Martínez-Palacios, R Xu… - … Therapy-Methods & …, 2022 - cell.com
Recessive dystrophic epidermolysis bullosa, a devastating skin fragility disease
characterized by recurrent skin blistering, scarring, and a high risk of developing squamous …