Outcome measures in hemophilia: current and future perspectives

S Benemei, L Boni, G Castaman - Expert Review of Hematology, 2024 - Taylor & Francis
Introduction Hemophilia can detrimentally affect patients' quality of life and likelihood of
survival. In the evolving landscape of therapies, the therapeutic gain of each treatment must …

Nonsevere Hemophilia: The Need for a Renewed Focus and Improved Outcomes

G Dolan, K Fijnvandraat, PJ Lenting… - … in Thrombosis and …, 2024 - thieme-connect.com
People with nonsevere hemophilia (PWNSH) are phenotypically more diverse than those
with severe hemophilia. Perceptions relating to a “nonsevere” phenotype have contributed …

[PDF][PDF] The imperative to prevent joint bleeding in everyone living with hemophilia

LA Valentino - Research and Practice in Thrombosis and …, 2024 - Elsevier
People with hemophilia (PwH) continue to experience bleeding and hemorrhage including
into their joints resulting arthropathy, disability and decreased health related quality of life …