Correction of alpha-1-antitrypsin genetic defects using spliceosome mediated RNA trans splicing

M Puttaraju, E Otto, MA Garcia-Blanco… - US Patent …, 2011 - Google Patents
The present invention provides methods and compositions for generating novel nucleic acid
molecules through targeted spliceosomal mediated RNA trans-splicing. The compositions of …

Correction of alpha-1-antitrypsin genetic defects using spliceosome mediated RNA trans splicing

M Puttaraju, E Otto, M Garcia-Blanco… - US Patent App. 11 …, 2006 - Google Patents
The present invention provides methods and compositions for generating novel nucleic acid
molecules through targeted spliceosomal mediated RNA trans-splicing. The compositions of …

Correction of alpha-1-antitrypsin genetic defects using spliceosome mediated RNA trans splicing

M Puttaraju, E Otto, MA Garcia-blanco… - US Patent …, 2011 - freepatentsonline.com
The present invention provides methods and compositions for generating novel nucleic acid
molecules through targeted spliceosomal mediated RNA trans-splicing. The compositions of …

Correction of alpha-1-antitrypsin genetic defects using spliceosome mediated RNA trans splicing

M Puttaraju, E Otto, MA Garcia-blanco… - US Patent App. 11 …, 2006 - freepatentsonline.com
The present invention provides methods and compositions for generating novel nucleic acid
molecules through targeted spliceosomal mediated RNA trans-splicing. The compositions of …