[PDF][PDF] Antisense oligonucleotide-mediated exon skipping strategies as the treatment for rare diseases

D Li - researchportal.murdoch.edu.au
Antisense oligomer-mediated exon skipping is being developed as a strategy for
personalised treatment of genetic disorders through excising “in-frame” exons carrying small …

Antisense oligonucleotide-mediated exon skipping strategies as the treatment for rare diseases

D Li - 2020 - researchportal.murdoch.edu.au
Antisense oligomer-mediated exon skipping is being developed as a strategy for
personalised treatment of genetic disorders through excising “in-frame” exons carrying small …