[HTML][HTML] Phase 1 gene therapy for Duchenne muscular dystrophy using a translational optimized AAV vector

DE Bowles, SWJ McPhee, C Li, SJ Gray, JJ Samulski… - Molecular Therapy, 2012 - cell.com
Efficient and widespread gene transfer is required for successful treatment of Duchenne
muscular dystrophy (DMD). Here, we performed the first clinical trial using a chimeric adeno …

Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector.

DE Bowles, SWJ McPhee, C Li, SJ Gray… - Molecular …, 2012 - search.ebscohost.com
Efficient and widespread gene transfer is required for successful treatment of Duchenne
muscular dystrophy (DMD). Here, we performed the first clinical trial using a chimeric adeno …

Phase 1 gene therapy for Duchenne muscular dystrophy using a translational optimized AAV vector

DE Bowles, SWJ McPhee, C Li… - … therapy: the journal …, 2012 - pubmed.ncbi.nlm.nih.gov
Efficient and widespread gene transfer is required for successful treatment of Duchenne
muscular dystrophy (DMD). Here, we performed the first clinical trial using a chimeric adeno …

Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

DE Bowles, SWJ McPhee, C Li, SJ Gray… - Molecular …, 2012 - cdr.lib.unc.edu
Efficient and widespread gene transfer is required for successful treatment of Duchenne
muscular dystrophy (DMD). Here, we performed the first clinical trial using a chimeric adeno …

[PDF][PDF] Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

DE Bowles, SWJ McPhee, C Li, SJ Gray… - Molecular …, 2012 - core.ac.uk
Duchenne muscular dystrophy (DMD) is the most common severe, life-threatening form of
muscular dystrophy in childhood. DMD is associated with progressive muscle degeneration …

Phase 1 gene therapy for Duchenne muscular dystrophy using a translational optimized AAV vector.

DE Bowles, SW McPhee, C Li, SJ Gray… - … Therapy: the Journal …, 2011 - europepmc.org
Efficient and widespread gene transfer is required for successful treatment of Duchenne
muscular dystrophy (DMD). Here, we performed the first clinical trial using a chimeric adeno …

[PDF][PDF] Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

DE Bowles, SWJ McPhee, C Li, SJ Gray, JJ Samulski… - researchgate.net
Duchenne muscular dystrophy (DMD) is the most common severe, life-threatening form of
muscular dystrophy in childhood. DMD is associated with progressive muscle degeneration …

Phase 1 gene therapy for duchenne muscular dystrophy using a translational optimized AAV vector

DE Bowles, SWJ McPhee, C Li… - Molecular …, 2012 - utsouthwestern.elsevierpure.com
Efficient and widespread gene transfer is required for successful treatment of Duchenne
muscular dystrophy (DMD). Here, we performed the first clinical trial using a chimeric adeno …

[HTML][HTML] Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

DE Bowles, SWJ McPhee, C Li, SJ Gray… - Molecular …, 2012 - ncbi.nlm.nih.gov
Efficient and widespread gene transfer is required for successful treatment of Duchenne
muscular dystrophy (DMD). Here, we performed the first clinical trial using a chimeric adeno …

Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

DE Bowles, SW Mcphee, C Li, SJ Gray… - Molecular …, 2012 - search.proquest.com
Efficient and widespread gene transfer is required for successful treatment of Duchenne
muscular dystrophy (DMD). Here, we performed the first clinical trial using a chimeric adeno …