Enzyme replacement therapy for lysosomal diseases: lessons from 20 years of experience and remaining challenges

RJ Desnick, EH Schuchman - Annual review of genomics and …, 2012 - annualreviews.org
In 1964, Christian de Duve first suggested that enzyme replacement might prove therapeutic
for lysosomal storage diseases (LSDs). Early efforts identified the major obstacles, including …

Enzyme Replacement Therapy for Lysosomal Diseases: Lessons from 20 Years of Experience and Remaining Challenges

RJ Desnick, EH Schuchman - Annual Review of Genomics and Human …, 2012 - cir.nii.ac.jp
抄録< jats: p> In 1964, Christian de Duve first suggested that enzyme replacement might
prove therapeutic for lysosomal storage diseases (LSDs). Early efforts identified the major …

Enzyme replacement therapy for lysosomal diseases: lessons from 20 years of experience and remaining challenges

RJ Desnick, EH Schuchman - Annual review of …, 2012 - pubmed.ncbi.nlm.nih.gov
In 1964, Christian de Duve first suggested that enzyme replacement might prove therapeutic
for lysosomal storage diseases (LSDs). Early efforts identified the major obstacles, including …

[PDF][PDF] Enzyme Replacement Therapy for Lysosomal Diseases: Lessons from 20 Years of Experience and Remaining Challenges

RJ Desnick, EH Schuchman - Annual Review of Genomics and …, 2012 - scholar.archive.org
Abstract In 1964, Christian de Duve first suggested that enzyme replacement might prove
therapeutic for lysosomal storage diseases (LSDs). Early efforts identified the major …

Enzyme replacement therapy for lysosomal diseases: lessons from 20 years of experience and remaining challenges.

RJ Desnick, EH Schuchman - Annual Review of Genomics and …, 2012 - europepmc.org
In 1964, Christian de Duve first suggested that enzyme replacement might prove therapeutic
for lysosomal storage diseases (LSDs). Early efforts identified the major obstacles, including …

[PDF][PDF] Enzyme Replacement Therapy for Lysosomal Diseases: Lessons from 20 Years of Experience and Remaining Challenges

RJ Desnick, EH Schuchman - Annual Review of Genomics and …, 2012 - scholar.archive.org
Abstract In 1964, Christian de Duve first suggested that enzyme replacement might prove
therapeutic for lysosomal storage diseases (LSDs). Early efforts identified the major …