Assessment of systemic delivery of rAAVrh74. MHCK7. micro-dystrophin in children with Duchenne muscular dystrophy: a nonrandomized controlled trial

JR Mendell, Z Sahenk, K Lehman, C Nease… - JAMA …, 2020 - jamanetwork.com
Importance Micro-dystrophin gene transfer shows promise for treating patients with
Duchenne muscular dystrophy (DMD) using recombinant adeno-associated virus serotype …
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[HTML][HTML] Assessment of Systemic Delivery of rAAVrh74. MHCK7. micro-dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial

JR Mendell, Z Sahenk, K Lehman, C Nease… - JAMA …, 2020 - ncbi.nlm.nih.gov
Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With
Duchenne Muscular Dystrophy - PMC Back to Top Skip to main content NIH NLM Logo Access …

Assessment of Systemic Delivery of rAAVrh74. MHCK7. micro-dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial.

JR Mendell, Z Sahenk, K Lehman, C Nease… - JAMA …, 2020 - search.ebscohost.com
This nonrandomized controlled trial analyzes safety, biological, and functional outcomes
associated with the infusion of rAAVrh74. MHCK7. micro-dystrophin gene transfer in a small …
[PDF] researchgate.net

[PDF][PDF] Assessment of Systemic Delivery of rAAVrh74. MHCK7. micro-dystrophin in Children With Duchenne Muscular Dystrophy A Nonrandomized Controlled Trial

JR Mendell, Z Sahenk, K Lehman, C Nease, LP Lowes… - researchgate.net
OBJECTIVE To identify the 1-year safety and tolerability of intravenous rAAVrh74. MHCK7.
micro-dystrophin in patients with DMD. DESIGN, SETTING, AND PARTICIPANTS This open …

Assessment of Systemic Delivery of rAAVrh74. MHCK7. micro-dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial

JR Mendell, Z Sahenk, K Lehman… - JAMA …, 2020 - pubmed.ncbi.nlm.nih.gov
Importance Micro-dystrophin gene transfer shows promise for treating patients with
Duchenne muscular dystrophy (DMD) using recombinant adeno-associated virus serotype …

Assessment of Systemic Delivery of rAAVrh74. MHCK7. micro-dystrophin in Children with Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial

JR Mendell, Z Sahenk, K Lehman… - JAMA …, 2020 - ohiostate.elsevierpure.com
Importance: Micro-dystrophin gene transfer shows promise for treating patients with
Duchenne muscular dystrophy (DMD) using recombinant adeno-Associated virus serotype …

[引用][C] Assessment of Systemic Delivery of rAAVrh74. MHCK7. micro-dystrophin in Children With Duchenne Muscular Dystrophy

JR Mendell, Z Sahenk, K Lehman, C Nease… - JAMA …, 2020 - cir.nii.ac.jp
Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With
Duchenne Muscular Dystrophy | CiNii Research CiNii 国立情報学研究所 学術情報ナビゲータ[サイニィ …

Assessment of Systemic Delivery of rAAVrh74. MHCK7. micro-dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial.

JR Mendell, Z Sahenk, K Lehman, C Nease… - JAMA …, 2020 - europepmc.org
Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With
Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial. - Abstract - Europe PMC …

Assessment of Systemic Delivery of rAAVrh74. MHCK7. micro-dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial.

JR Mendell, Z Sahenk, K Lehman, C Nease… - JAMA …, 2020 - europepmc.org
Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With
Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial. - Abstract - Europe PMC …