Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
J McIntosh, PJ Lenting, C Rosales… - Blood, The Journal …, 2013 - ashpublications.org
Recombinant adeno-associated virus (rAAV) vectors encoding human factor VIII (hFVIII)
were systematically evaluated for hemophilia A (HA) gene therapy. A 5.7-kb rAAV …
were systematically evaluated for hemophilia A (HA) gene therapy. A 5.7-kb rAAV …
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
J McIntosh, PJ Lenting, C Rosales, D Lee… - Blood, 2013 - cir.nii.ac.jp
抄録< jats: title> Key Points</jats: title>< jats: p> Novel, more potent codon-optimized human
FVIII variant (codop-hFVIII-V3). Codop-hFVIII-V3 is safe and efficacious in mice and …
FVIII variant (codop-hFVIII-V3). Codop-hFVIII-V3 is safe and efficacious in mice and …
[PDF][PDF] Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
J McIntosh, PJ Lenting, C Rosales, D Lee… - therapy, 2013 - academia.edu
Hemophilia A (HA), the most common inherited bleeding disorder, caused by a deficiency of
factor VIII (FVIII) is well suited for a gene replacement approach, primarily because a modest …
factor VIII (FVIII) is well suited for a gene replacement approach, primarily because a modest …
[PDF][PDF] Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
J McIntosh, PJ Lenting, C Rosales, D Lee… - therapy, 2013 - researchgate.net
Hemophilia A (HA), the most common inherited bleeding disorder, caused by a deficiency of
factor VIII (FVIII) is well suited for a gene replacement approach, primarily because a modest …
factor VIII (FVIII) is well suited for a gene replacement approach, primarily because a modest …
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
J McIntosh, PJ Lenting, C Rosales, D Lee… - …, 2013 - pubmed.ncbi.nlm.nih.gov
Recombinant adeno-associated virus (rAAV) vectors encoding human factor VIII (hFVIII)
were systematically evaluated for hemophilia A (HA) gene therapy. A 5.7-kb rAAV …
were systematically evaluated for hemophilia A (HA) gene therapy. A 5.7-kb rAAV …
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant.
J McIntosh, PJ Lenting, C Rosales, D Lee… - Blood, 2013 - europepmc.org
Recombinant adeno-associated virus (rAAV) vectors encoding human factor VIII (hFVIII)
were systematically evaluated for hemophilia A (HA) gene therapy. A 5.7-kb rAAV …
were systematically evaluated for hemophilia A (HA) gene therapy. A 5.7-kb rAAV …
[HTML][HTML] Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
J McIntosh, PJ Lenting, C Rosales, D Lee… - Blood, 2013 - ncbi.nlm.nih.gov
Recombinant adeno-associated virus (rAAV) vectors encoding human factor VIII (hFVIII)
were systematically evaluated for hemophilia A (HA) gene therapy. A 5.7-kb rAAV …
were systematically evaluated for hemophilia A (HA) gene therapy. A 5.7-kb rAAV …
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
J McIntosh, PJ Lenting, C Rosales, D Lee… - …, 2013 - openresearch.surrey.ac.uk
Science & Technology Life Sciences & Biomedicine Hematology HEMATOLOGY
ADENOASSOCIATED VIRAL VECTORS RECOMBINANT FACTOR-VIII MEDIATED GENE …
ADENOASSOCIATED VIRAL VECTORS RECOMBINANT FACTOR-VIII MEDIATED GENE …
[HTML][HTML] Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
J McIntosh, PJ Lenting, C Rosales, D Lee… - Blood, 2013 - Elsevier
Recombinant adeno-associated virus (rAAV) vectors encoding human factor VIII (hFVIII)
were systematically evaluated for hemophilia A (HA) gene therapy. A 5.7-kb rAAV …
were systematically evaluated for hemophilia A (HA) gene therapy. A 5.7-kb rAAV …
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
J McIntosh, PJ Lenting, C Rosales, D Lee… - …, 2013 - openresearch.surrey.ac.uk
Science & Technology Life Sciences & Biomedicine Hematology HEMATOLOGY
ADENOASSOCIATED VIRAL VECTORS RECOMBINANT FACTOR-VIII MEDIATED GENE …
ADENOASSOCIATED VIRAL VECTORS RECOMBINANT FACTOR-VIII MEDIATED GENE …