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Fatal thrombotic microangiopathy case following adeno-associated viral SMN gene therapy

J Guillou, A De Pellegars, F Porcheret… - Blood …, 2022 - ashpublications.org
Adeno-associated virus (AAV) gene therapies are highly promising, such as the
onasemnogene abeparvovec (Zolgensma) in spinal muscle atrophy (SMA). We report the …
被引用次数：81 相关文章

Fatal thrombotic microangiopathy case following adeno-associated viral SMN gene therapy.

J Guillou, A de Pellegars, F Porcheret… - Blood …, 2022 - europepmc.org
Adeno-associated virus (AAV) gene therapies are highly promising, such as the
onasemnogene abeparvovec (Zolgensma) in spinal muscle atrophy (SMA). We report the …
[HTML] nih.gov

[HTML][HTML] Fatal thrombotic microangiopathy case following adeno-associated viral SMN gene therapy

J Guillou, A de Pellegars, F Porcheret… - Blood …, 2022 - ncbi.nlm.nih.gov
Adeno-associated virus (AAV) gene therapies are highly promising, such as the
onasemnogene abeparvovec (Zolgensma) in spinal muscle atrophy (SMA). We report the …

Fatal thrombotic microangiopathy case following adeno-associated viral SMN gene therapy

J Guillou, A de Pellegars, F Porcheret… - Blood …, 2022 - pubmed.ncbi.nlm.nih.gov
Adeno-associated virus (AAV) gene therapies are highly promising, such as the
onasemnogene abeparvovec (Zolgensma) in spinal muscle atrophy (SMA). We report the …
[HTML] sciencedirect.com

[HTML][HTML] Fatal thrombotic microangiopathy case following adeno-associated viral SMN gene therapy

J Guillou, A de Pellegars, F Porcheret… - Blood Advances, 2022 - Elsevier
Adeno-associated virus (AAV) gene therapies are highly promising, such as the
onasemnogene abeparvovec (Zolgensma) in spinal muscle atrophy (SMA). We report the …