Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

N Cartier, S Hacein-Bey-Abina, CC Bartholomae… - science, 2009 - science.org
X-linked adrenoleukodystrophy (ALD) is a severe brain demyelinating disease in boys that
is caused by a deficiency in ALD protein, an adenosine triphosphate–binding cassette …

[PDF][PDF] Hematopoietic Stem Cell Gene Therapy with

N Cartier - science, 2009 - researchgate.net
X-linked adrenoleukodystrophy (ALD) is a severe brain demyelinating disease in boys that
is caused by a deficiency in ALD protein, an adenosine triphosphate–binding cassette …

[引用][C] Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy

N CARTIER, S HACEIN-BEY-ABINA… - Science …, 2009 - pascal-francis.inist.fr
Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked
Adrenoleukodystrophy CNRS Inist Pascal-Francis CNRS Pascal and Francis Bibliographic …

Hematopoietic stem cell Gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

N Cartier, S Hacein-Bey-Abina, CC Bartholomae… - Science, 2009 - cea.hal.science
X-linked adrenoleukodystrophy (ALD) is a severe brain demyelinating disease in boys that
is caused by a deficiency in ALD protein, an adenosine triphosphate–binding cassette …

[PDF][PDF] Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

N Cartier, S Hacein-Bey-Abina, CC Bartholomae… - Science, 2009 - scholar.archive.org
Background: X-linked adrenoleukodystrophy (ALD) is a severe brain demyelinating disease
in boys that is caused by a deficiency in ALD protein, an adenosine triphosphate-binding …

Hematopoietic stem cell Gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

N Cartier, S Hacein-Bey-Abina, CC Bartholomae… - Science, 2009 - inria.hal.science
X-linked adrenoleukodystrophy (ALD) is a severe brain demyelinating disease in boys that
is caused by a deficiency in ALD protein, an adenosine triphosphate–binding cassette …

Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy

N Cartier, S Hacein-Bey-Abina, CC Bartholomae… - Science, 2009 - ui.adsabs.harvard.edu
X-linked adrenoleukodystrophy (ALD) is a severe brain demyelinating disease in boys that
is caused by a deficiency in ALD protein, an adenosine triphosphate-binding cassette …

Hematopoietic stem cell Gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

N Cartier, S Hacein-Bey-Abina, CC Bartholomae… - Science, 2009 - hal-ciheam.iamm.fr
X-linked adrenoleukodystrophy (ALD) is a severe brain demyelinating disease in boys that
is caused by a deficiency in ALD protein, an adenosine triphosphate–binding cassette …

Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy

N Cartier, S Hacein-Bey-Abina, CC Bartholomae… - Science, 2009 - JSTOR
X-linked adrenoleukodystrophy (ALD) is a severe brain demyelinating disease in boys that
is caused by a deficiency in ALD protein, an adenosine triphosphate–binding cassette …

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

N Cartier, S Hacein-Bey-Abina… - … (New York, NY), 2009 - pubmed.ncbi.nlm.nih.gov
X-linked adrenoleukodystrophy (ALD) is a severe brain demyelinating disease in boys that
is caused by a deficiency in ALD protein, an adenosine triphosphate-binding cassette …