Do you know the sex of your cells?

K Shah, CE McCormack… - American Journal of …, 2014 - journals.physiology.org
Do you know the sex of your cells? Not a question that is frequently heard around the lab
bench, yet thanks to recent research is probably one that should be asked. It is self-evident …

Chaperoning G protein-coupled receptors: from cell biology to therapeutics

YX Tao, PM Conn - Endocrine reviews, 2014 - academic.oup.com
G protein-coupled receptors (GPCRs) are membrane proteins that traverse the plasma
membrane seven times (hence, are also called 7TM receptors). The polytopic structure of …

A CFTR corrector (lumacaftor) and a CFTR potentiator (ivacaftor) for treatment of patients with cystic fibrosis who have a phe508del CFTR mutation: a phase 2 …

MP Boyle, SC Bell, MW Konstan… - The lancet Respiratory …, 2014 - thelancet.com
Background The phe508del CFTR mutation causes cystic fibrosis by limiting the amount of
CFTR protein that reaches the epithelial cell surface. We tested combination treatment with …

[HTML][HTML] Effect of ivacaftor on CFTR forms with missense mutations associated with defects in protein processing or function

F Van Goor, H Yu, B Burton, BJ Hoffman - Journal of Cystic Fibrosis, 2014 - Elsevier
Abstract Background Ivacaftor (KALYDECO™, VX-770) is a CFTR potentiator that increased
CFTR channel activity and improved lung function in patients age 6 years and older with CF …

Some gating potentiators, including VX-770, diminish ΔF508-CFTR functional expression

G Veit, RG Avramescu, D Perdomo… - Science translational …, 2014 - science.org
Cystic fibrosis (CF) is caused by mutations in the CF transmembrane regulator (CFTR) that
result in reduced anion conductance at the apical membrane of secretory epithelia …

CFTR: cystic fibrosis and beyond

MA Mall, D Hartl - 2014 - Eur Respiratory Soc
Cystic fibrosis (CF) remains the most common fatal hereditary lung disease. The discovery of
the cystic fibrosis transmembrane conductance regulator (CFTR) gene 25 years ago set the …

Potentiator ivacaftor abrogates pharmacological correction of ΔF508 CFTR in cystic fibrosis

DM Cholon, NL Quinney, ML Fulcher… - Science translational …, 2014 - science.org
Cystic fibrosis (CF) is caused by mutations in the CF transmembrane conductance regulator
(CFTR). Newly developed “correctors” such as lumacaftor (VX-809) that improve CFTR …

[HTML][HTML] Glucose-induced electrical activities and insulin secretion in pancreatic islet β-cells are modulated by CFTR

JH Guo, H Chen, YC Ruan, XL Zhang… - Nature …, 2014 - nature.com
The cause of insulin insufficiency remains unknown in many diabetic cases. Up to 50% adult
patients with cystic fibrosis (CF), a disease caused by mutations in the gene encoding the …

Restoration of CFTR function in patients with cystic fibrosis carrying the F508del-CFTR mutation

DD Stefano, VR Villella, S Esposito, A Tosco, A Sepe… - Autophagy, 2014 - Taylor & Francis
Restoration of BECN1/Beclin 1-dependent autophagy and depletion of SQSTM1/p62 by
genetic manipulation or autophagy-stimulatory proteostasis regulators, such as cystamine …

Synthetic aminoglycosides efficiently suppress cystic fibrosis transmembrane conductance regulator nonsense mutations and are enhanced by ivacaftor

X Xue, V Mutyam, L Tang, S Biswas, M Du… - American journal of …, 2014 - atsjournals.org
New drugs are needed to enhance premature termination codon (PTC) suppression to treat
the underlying cause of cystic fibrosis (CF) and other diseases caused by nonsense …