PMO-based let-7c site blocking oligonucleotide (SBO) mediated utrophin upregulation in mdx mice, a therapeutic approach for Duchenne muscular dystrophy (DMD)

K Sengupta, E Loro, TS Khurana - Scientific Reports, 2020 - nature.com
Upregulation of utrophin, a dystrophin related protein, is considered a promising therapeutic
approach for Duchenne muscular dystrophy (DMD). Utrophin expression is repressed at the …