Idebenone Treatment in Patients with OPA1-Dominant Optic Atrophy: A Prospective Phase 2 Trial

K Valentin, T Georgi, R Riedl, H Aminfar… - Neuro …, 2023 - Taylor & Francis
The aim of this study was to evaluate the therapeutic effect of idebenone in patients with
OPA1-dominant optic atrophy (DOA). Sixteen patients with genetically confirmed OPA1-DOA …