[HTML][HTML] mRNA-based therapeutics—developing a new class of drugs

U Sahin, K Karikó, Ö Türeci - Nature reviews Drug discovery, 2014 - nature.com
In vitro transcribed (IVT) mRNA has recently come into focus as a potential new drug class to
deliver genetic information. Such synthetic mRNA can be engineered to transiently express …

Nanotechnologies in delivery of mRNA therapeutics using nonviral vector-based delivery systems

S Guan, J Rosenecker - Gene therapy, 2017 - nature.com
Because of its safe and effective protein expression profile, in vitro transcribed messenger
RNA (IVT-mRNA) represents a promising candidate in the development of novel …

Molecular evolution of a novel hyperactive Sleeping Beauty transposase enables robust stable gene transfer in vertebrates

L Mátés, MKL Chuah, E Belay, B Jerchow, N Manoj… - Nature …, 2009 - nature.com
Abstract The Sleeping Beauty (SB) transposon is a promising technology platform for gene
transfer in vertebrates; however, its efficiency of gene insertion can be a bottleneck in …

Contemporary Transposon Tools: A Review and Guide through Mechanisms and Applications of Sleeping Beauty, piggyBac and Tol2 for Genome Engineering

N Sandoval-Villegas, W Nurieva, M Amberger… - International journal of …, 2021 - mdpi.com
Transposons are mobile genetic elements evolved to execute highly efficient integration of
their genes into the genomes of their host cells. These natural DNA transfer vehicles have …

Sarcoma derived from cultured mesenchymal stem cells

J Tolar, AJ Nauta, MJ Osborn… - Stem …, 2007 - academic.oup.com
To study the biodistribution of MSCs, we labeled adult murine C57BL/6 MSCs with firefly
luciferase and DsRed2 fluorescent protein using nonviral Sleeping Beauty transposons and …

Transposon-mediated genome manipulation in vertebrates

Z Ivics, MA Li, L Mátés, JD Boeke, A Nagy, A Bradley… - Nature …, 2009 - nature.com
Transposable elements are DNA segments with the unique ability to move about in the
genome. This inherent feature can be exploited to harness these elements as gene vectors …

Gene transfer into genomes of human cells by the sleeping beauty transposon system

AM Geurts, Y Yang, KJ Clark, G Liu, Z Cui, AJ Dupuy… - Molecular Therapy, 2003 - cell.com
Abstract The Sleeping Beauty (SB) transposon system, derived from teleost fish sequences,
is extremely effective at delivering DNA to vertebrate genomes, including those of humans …

Harnessing a high cargo-capacity transposon for genetic applications in vertebrates

D Balciunas, KJ Wangensteen, A Wilber, J Bell… - PLoS …, 2006 - journals.plos.org
Viruses and transposons are efficient tools for permanently delivering foreign DNA into
vertebrate genomes but exhibit diminished activity when cargo exceeds 8 kilobases (kb) …

High-resolution genome-wide mapping of transposon integration in mammals

SR Yant, X Wu, Y Huang, B Garrison… - … and cellular biology, 2005 - Am Soc Microbiol
Abstract The Sleeping Beauty (SB) transposon is an emerging tool for transgenesis, gene
discovery, and therapeutic gene delivery in mammals. Here we studied 1,336 SB insertions …

Sleeping beauty transposition: biology and applications for molecular therapy

Z Izsvák, Z Ivics - Molecular Therapy, 2004 - cell.com
Transposable elements can be considered as natural, nonviral gene-delivery vehicles and
are valuable and widely used tools for germ-line transgenesis and insertional mutagenesis …