[HTML][HTML] PMO-based let-7c site blocking oligonucleotide (SBO) mediated utrophin upregulation in mdx mice, a therapeutic approach for Duchenne muscular …

K Sengupta, E Loro, TS Khurana - Scientific Reports, 2020 - nature.com
Upregulation of utrophin, a dystrophin related protein, is considered a promising therapeutic
approach for Duchenne muscular dystrophy (DMD). Utrophin expression is repressed at the …

Muscular Dystrophy: Mutations in the Dystrophin Gene

A Agarwal, K Verma, S Tyagi, K Gupta… - Mechanism and Genetic …, 2024 - Springer
Muscular dystrophy (MD) is a heterogeneous group of genetic disorders characterized by
progressive muscle degeneration and weakness, leading to significant morbidity and …