Mutations in G protein–coupled receptors: mechanisms, pathophysiology and potential therapeutic approaches

T Schöneberg, I Liebscher, P Insel - Pharmacological reviews, 2021 - Elsevier
There are approximately 800 annotated G protein–coupled receptor (GPCR) genes, making
these membrane receptors members of the most abundant gene family in the human …

The role of GPCRs in bone diseases and dysfunctions

J Luo, P Sun, S Siwko, M Liu, J Xiao - Bone research, 2019 - nature.com
The superfamily of G protein-coupled receptors (GPCRs) contains immense structural and
functional diversity and mediates a myriad of biological processes upon activation by …

Phenotypic expansion illuminates multilocus pathogenic variation

E Karaca, JE Posey, Z Coban Akdemir… - Genetics in …, 2018 - nature.com
Purpose Multilocus variation—pathogenic variants in two or more disease genes—can
potentially explain the underlying genetic basis for apparent phenotypic expansion in cases …

Adhesion G protein-coupled receptors: opportunities for drug discovery

F Bassilana, M Nash, MG Ludwig - Nature reviews Drug discovery, 2019 - nature.com
Adhesion G protein-coupled receptors (aGPCRs)—one of the five main families in the GPCR
superfamily—have several atypical characteristics, including large, multi-domain N termini …

Ligands and beyond: Mechanosensitive adhesion GPCRs

HH Lin, KF Ng, TC Chen, WY Tseng - Pharmaceuticals, 2022 - mdpi.com
Cells respond to diverse types of mechanical stimuli using a wide range of plasma
membrane-associated mechanosensitive receptors to convert extracellular mechanical cues …

A CCG expansion in ABCD3 causes oculopharyngodistal myopathy in individuals of European ancestry

A Cortese, SJ Beecroft, S Facchini, R Curro… - Nature …, 2024 - nature.com
Oculopharyngodistal myopathy (OPDM) is an inherited myopathy manifesting with ptosis,
dysphagia and distal weakness. Pathologically it is characterised by rimmed vacuoles and …

Peripheral nervous system (PNS) myelin diseases

SS Scherer, J Svaren - Cold Spring Harbor Perspectives …, 2024 - cshperspectives.cshlp.org
This is a review of inherited and acquired causes of human demyelinating neuropathies and
a subset of disorders that affect axon–Schwann cell interactions. Nearly all inherited …

Adhesion G protein–coupled receptors as drug targets

RH Purcell, RA Hall - Annual review of pharmacology and …, 2018 - annualreviews.org
The adhesion G protein–coupled receptors (aGPCRs) are an evolutionarily ancient family of
receptors that play key roles in many different physiological processes. These receptors are …

The function of the cellular prion protein in health and disease

JC Watts, MEC Bourkas, H Arshad - Acta neuropathologica, 2018 - Springer
The essential role of the cellular prion protein (PrP C) in prion disorders such as Creutzfeldt–
Jakob disease is well documented. Moreover, evidence is accumulating that PrP C may act …

Next generation sequencing in a large cohort of patients presenting with neuromuscular disease before or at birth

EJ Todd, KS Yau, R Ong, J Slee, G McGillivray… - Orphanet Journal of …, 2015 - Springer
Background Fetal akinesia/hypokinesia, arthrogryposis and severe congenital myopathies
are heterogeneous conditions usually presenting before or at birth. Although numerous …